Simultaneous Control of Endogenous and User-Defined Genetic Pathways Using Unique ecDHFR Pharmacological Chaperones

Prerana Ramadurgum, Da Nae R. Woodard, Steffi Daniel, Hui Peng, Prema L. Mallipeddi, Hanspeter Niederstrasser, Melina Mihelakis, Viet Q. Chau, Peter M. Douglas, Bruce A. Posner, John D. Hulleman

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