Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder

Felix Nitschke; Alina P. Montalbano

doi:10.1007/s13311-022-01314-8

Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder

Felix Nitschke, Alina P. Montalbano

Research output: Contribution to journal › Comment/debate › peer-review

Original language	English (US)
Journal	Neurotherapeutics
DOIs	https://doi.org/10.1007/s13311-022-01314-8
State	Accepted/In press - 2022

Keywords

AAVPHP
CDKL5 deficiency
Cross-correction
Enzyme replacement therapy
Gene replacement therapy
TAT

ASJC Scopus subject areas

Pharmacology
Clinical Neurology
Pharmacology (medical)

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10.1007/s13311-022-01314-8

Cite this

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title = "Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder",

keywords = "AAVPHP, CDKL5 deficiency, Cross-correction, Enzyme replacement therapy, Gene replacement therapy, TAT",

author = "Felix Nitschke and Montalbano, {Alina P.}",

year = "2022",

doi = "10.1007/s13311-022-01314-8",

language = "English (US)",

journal = "Neurotherapeutics",

issn = "1933-7213",

publisher = "Springer New York",

}

TY - JOUR

T1 - Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder

AU - Nitschke, Felix

AU - Montalbano, Alina P.

PY - 2022

Y1 - 2022

KW - AAVPHP

KW - CDKL5 deficiency

KW - Cross-correction

KW - Enzyme replacement therapy

KW - Gene replacement therapy

KW - TAT

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U2 - 10.1007/s13311-022-01314-8

DO - 10.1007/s13311-022-01314-8

M3 - Comment/debate

C2 - 36266502

AN - SCOPUS:85140250690

SN - 1933-7213

JO - Neurotherapeutics

JF - Neurotherapeutics

ER -

Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder

Keywords

ASJC Scopus subject areas

Access to Document

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