Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy

Leonela Amoasii, John C.W. Hildyard, Hui Li, Efrain Sanchez-Ortiz, Alex Mireault, Daniel Caballero, Rachel Harron, Thaleia Rengina Stathopoulou, Claire Massey, John M. Shelton, Rhonda Bassel-Duby, Richard J. Piercy, Eric N. Olson

Research output: Contribution to journalArticlepeer-review

372 Scopus citations

Fingerprint

Dive into the research topics of 'Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy'. Together they form a unique fingerprint.

Medicine & Life Sciences