Editorial: Lessons Learned from Translational Research in Neuromuscular Diseases: Impact on Study Design, Outcome Measures and Managing Expectation

Anna G. Mayhew, Leslie Nelson, Michela Guglieri, Tracey Willis

Research output: Contribution to journalEditorialpeer-review

1 Scopus citations
Original languageEnglish (US)
Article number840074
JournalFrontiers in Genetics
Volume13
DOIs
StatePublished - Jul 4 2022

Keywords

  • clinical outcome assessments
  • clinical trial
  • duchenne muscular dystrophy (DMD)
  • neuromuscular disorders (NMD)
  • remote assessment
  • spinal muscular atrophy (SMA)

ASJC Scopus subject areas

  • Molecular Medicine
  • Genetics
  • Genetics(clinical)

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