Biodistribution of Adeno-Associated Virus Gene Therapy Following Cerebrospinal Fluid-Directed Administration

Xin Chen, Daniel A. Lim, Michael W. Lawlor, David Dimmock, Charles H. Vite, Thomas Lester, Fatemeh Tavakkoli, Chanchal Sadhu, Suyash Prasad, Steven J. Gray

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Medicine & Life Sciences