All-In-One Dendrimer-Based Lipid Nanoparticles Enable Precise HDR-Mediated Gene Editing In Vivo

Lukas Farbiak, Qiang Cheng, Tuo Wei, Ester Álvarez-Benedicto, Lindsay T. Johnson, Sang Lee, Daniel J. Siegwart

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54 Scopus citations

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Engineering & Materials Science

Chemical Compounds