Network
Mauricio R Delgado-Ayala
- Neurology & Neurotherapeutics - Professor (Nontenured Clinical)
- Neurology & Neurotherapeutics - NE Outside Agreements
Person: Academic
Anil K Agarwal
- Internal Medicine - Professor (Nontenured Research)
- Int Med - Nutrition & Met Dis
Person: Academic
Lin Xu
- Pediatrics
- Pediatric Residency
- Peter O'Donnell Jr. School of Public Health - Assistant Professor
- SPH-Data Sciences in Precision
Person: Academic
Yanbin Zheng
- Pediatrics - Assistant Professor (Nontenured Research)
- Hematology & Oncology
Person: Academic
Richard S. Finkel
- Children's Hospital of Philadelphia
- Bambino Gesu' Childrens Research Hospital
- University of Pennsylvania
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Division of Neurology
- Departments of Neurology and Pediatrics
- Nemours
- Nemours Children's Clinic
- University of Central Florida
- Division of Neurology
- Division of Neurology
- Pediatric Neurology
- Department of Laboratories
- The Pediatric Neuromuscular Clinical Research Network
- Tel Aviv University
- St. Jude Children Research Hospital
- The Children's Hospital of Philadelphia
External person
B. S. Russman
- Cincinnati University Medical Center
- Newington Children's Hospital
- University of Connecticut
- Shriners Hospital for Children
- Oregon Health Sciences University
- Shriner's Hospital
- Shriners Hosp. for Children-Portland
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Texas Scottish Rite Hosp. Children
- Connecticut Children's Medical Center
- Shriners Hospitals for Children
- Oregon Health and Science University
- Department of Neurology
- Division of Pediatric
- Depts. of Pediatrics and Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Connecticut Children's Medical Center
- Department of Neurology
- Shriners Hospital
- Scottish Rite Hospital for Children
- University of Connecticut
- Children's Hospital New Orleans
External person
F. J. Samaha
- Cincinnati University Medical Center
- Newington Children's Hospital
- Univ. of Cincinnati Medical Center
- University of Cincinnati
- Cincinnati Children's Hosp. Med. C.
- University of Cincinnati Medical Center
- Texas Scottish Rite Hospital for Children
- Cincinnati Children's Hospital Medical Center
- Texas Scottish Rite Hosp. Children
- Connecticut Children's Medical Center
- Department of Neurology
- Division of Pediatric
- Department of Emergency Medicine
- Department of Neurology
- Connecticut Children's Medical Center
- Department of Neurology
- Scottish Rite Hospital for Children
- Department of Neurology
External person
Francesco Muntoni
- Hammersmith Hospital
- Istituto Ortopedico Rizzoli
- Great Ormond Street Hospital for Children
- Bambino Gesu' Childrens Research Hospital
- University College
- Dubowitz Neuromuscular Centre
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- University College London
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Imperial College London
- Dubowitz Neuromuscular Centre
- Dept. of Paediatr. and Neonatal Med.
- Neuromuscular Unit
- Department of Paediatrics
- Dubowitz Neuromuscular Centre
- Department of Laboratories
- Neurosciences Unit
- Imperial College Healthcare NHS Trust
- Moorfield's Eye Institute of London
- Great Ormond Street Hospital for Children Foundation Trust
External person
Kevin E. Bove
- Cincinnati Children's Hospital Medical Center
- Children's Hospital Medical Center
- Children's Hospital Research Foundation
- University of Louisville
- University of Cincinnati
- University of Cincinnati Medical Center
- Children's Hospital Medical Center Cincinnati
- The Children's Hospital Medical Center
- Cincinnati Children's Hospital
- Department of Pathology
- Department of Pathology and Laboratory Medicine
- Division of Neurology
- Division of Gastroenterology
- Division of Pathology
- Division of Nutrition
- Division of Cytopathology
- Department of Pathology
- Department of Pathology
- Department of Pathology
- Department of Pathology and Division of Pediatric Neurology
- Departments of Pediatrics and Neurology
- Division of Pathology
External person
Craig Mcdonald
- University of California at Davis
- Santhera Pharmaceuticals
- UC Davis Children's Hospital
External person
Basil T. Darras
- Harvard University
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Columbia University
- Spinal Muscular Atrophy Foundation
- Department of Neurology
- Boston Children's Hospital
- Johns Hopkins University
External person
Anne M. Connolly
- Washington University St. Louis
- Washington Univ. Sch. of Med.
- Washington Univ. School of Medicine
- Department of Neurology
- St. Louis Children’s Hospital
- Department of Neurology
- Rush University
- Neurology/Neurosurgery Intensive Care Unit
- Departments of Neurology and Pediatrics
- Department of Pediatrics
- Department of Neurology
- Spinal Muscular Atrophy Foundation
- Queen Fabiola Children's University Hospital
- Department of Neurology
- Department of Pediatrics
- Ohio State University
- Nationwide Children’s Hospital
External person
Nancy Kuntz
- Mayo Clinic Rochester, MN
- Children's Memorial Hospital
- Ann and Robert H. Lurie Children's Hospital of Chicago
- Department of Pediatrics
- Department of Neurology
- Northwestern University
- Department of Pediatrics
- Tel Aviv University
- Department of Pediatrics
- Ann & Robert H. Lurie Children's Hospital
External person
Kathryn Swoboda
- University of Utah
- Harvard University
- Bambino Gesu' Childrens Research Hospital
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Department of Neurology
- Departments of Neurology and Pediatrics
- Department of Neurology
- Genetics Division
- Department of Neurology
- Division of Genetics
- Department of Laboratories
- Department of Neurology
- Columbia University
- Departments of Neurology and Pediatrics
- Department of Pediatrics
- Department of Human Genetics
- Department of Neurology
- Boston Children's Hospital
- Massachusetts General Hospital
External person
Carsten G. Bönnemann
- National Institutes of Health
- Children's Hospital of Philadelphia
- University of Pennsylvania School of Medicine
- National Institutes of Health, Bethesda
- University of Pennsylvania
- Neurogenetics Branch
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Division of Neurology
- Division of Neurology
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- The Children's Hospital of Philadelphia
External person
Eugenio Mercuri
- Catholic University
- Bambino Gesu' Childrens Research Hospital
- Catholic University of the Sacred Heart
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Policlinico Universitario Agostino Gemelli
- Department of Pediatric Neurology
- Paediatric Neurology Unit
- Pediatric Neurology
- Department of Laboratories
- Pediatric Neurology Unit
- Child Neurology Unit
- Imperial College London
- Department of Paediatrics
- Hammersmith Hospital
- Pediatric Neurology Unit
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
External person
J. Kirschner
- University of Freiburg
- Department of Neuropediatrics and Muscle Disorders
- University of Bonn
- Freiberg University of Mining and Technology
External person
Perry B. Shieh
- University of California at Los Angeles
- Neurogenetics Program
- Department of Neurology
- Akron Children's Hospital
- Akron Children's Hospital
- University of Texas at Dallas
- Chinese University of Hong Kong
- University of Pittsburgh
External person
Claudia A. Chiriboga
- Columbia University
- Departments of Neurology
- Department of Neurology
- Department of Neurology
- Department of Pediatrics
- Cornell University
- New York Presbyterian Hospital
External person
Nigel G. Laing
- QEII Medical Centre
- University of Western Australia
- Harvard University
- Queen Elizabeth II Medical Centre Trust
- Australian Neuromuscular Research Institute
- Ctr. Neuromuscular/Neurol. Disord.
- Centre for Medical Research
- Genetics Division
- Ctr. for Neuromusc./Neurol. Disord.
- Harry Perkins Institute of Medical Research
- QEII Medical Centre
- Queen Elizabeth II Medical Centre Trust
- Boston Children's Hospital
External person
Thomas Sejersen
- Karolinska Institutet
- Astrid Lindgren Children Hospital
- Department of Women's and Children's Health
- Pediatric Neurology
- Department of Women's and Children's Health
- Astrid Lindgren Children Hospital
External person
Monique M. Ryan
- Harvard University
- Murdoch Children's Research Institute
- University of Melbourne
- Roy. Alexandra Hospital for Children
- Royal Children's Hospital
- Murdoch Children's Research Institute, Royal Children's Hospital
- University of Sydney
- Genetics Division
- Department of Neurology
- Neurogenetics Research Unit
- Neurosciences Department
- Children's Neuroscience Centre
- Department of Paediatrics
- Department of Neurology
- Neuroscience Research
- Department of Neurology
- Department of Paediatrics and Child Health
- Genom. Prog. and Div. of Genetics
- Children's Hospital
- Tel Aviv University
- The Children's Hospital at Westmead
- Boston Children's Hospital
External person
T. Voit
- Istituto Ortopedico Rizzoli
- Bambino Gesu' Childrens Research Hospital
- CNRS UMR 7215
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- CNRS
- Sorbonne Université
- University College London
- Neuromuscular Unit
- Institut de Myologie
- Department of Laboratories
- CNRS Centre National de la Recherche Scientifique
- Institut national de la santé et de la recherche médicale
- Universite Pierre et Marie Curie
- Thérapie des maladies du muscle strié
- University of Duisburg-Essen
- Department of Pediatrics
- Institut de Myologie
- National Institute for Health and Care Research
- ComUE Paris-Saclay
- Sorbonne Universités
- Great Ormond Street Hospital for Children Foundation Trust
External person
Erik Henricson
- George Washington University
- University of California
- University of California at Davis
- UC Davis Children's Hospital
External person
J. R. Mendell
- Nationwide Children's Hospital
- Ohio State University
- The Ohio State University
- Nationwide Children’s Hospital
- Department of Neurology
- Department of Neurology
- Center for Gene Therapy
- Department of Pediatrics
- Center for Gene Therapy
- Departments of Neurology and Pediatrics
- Department of Pediatrics
- Research Institute
- Departments of Biochemistry, Plant Biology
External person
R. J. Sokol
- University of Pittsburgh
- University of Colorado Denver
- Univ. of Colorado Hlth. Sci. Center
- Children's Hospital Medical Center
- Cincinnati Children's Hospital Medical Center
- Univ. of Colorado School of Medicine
- Children's Hospital Denver
- Children’s Hospital
- Mt. Sinai Medical Center
- Pediatric Liver Ctr. and Hepatobil. Research Ctr.
- Division of Neurology
- Division of Gastroenterology
- Division of Pathology
- Division of Nutrition
- Department of Pediatrics
- The EMMES Corporation
- Department of Pediatric Gastroenterology and Hepatology
- General Clinical Research Center
- Pediatric Liver Center
- Dept. of Peds.
- Sect. of Pediat. GI/Hepatology/Nutr.
- The EMMES Corporation
- University of Cincinnati
- University of Colorado Anschutz Medical Campus
- University of Pennsylvania
- Children's Memorial Hospital
- University of Michigan, Ann Arbor
- Johns Hopkins University
- Icahn School of Medicine at Mount Sinai
- University of California at San Francisco
- National Institutes of Health
- Washington University St. Louis
- The Children's Hospital of Philadelphia
- National Jewish Health and University of Colorado
External person
M. L. White
- Cincinnati University Medical Center
- Univ. of Cincinnati Medical Center
- University of Cincinnati
- Texas Scottish Rite Hospital for Children
- Newington Children's Hospital
- Connecticut Children's Medical Center
- Cincinnati Children's Hospital Medical Center
- Department of Neurology
- Department of Environmental Health
- Department of Epidemiology
- Department of Epidemiology
- Connecticut Children's Medical Center
- Scottish Rite Hospital for Children
External person
Alan H. Beggs
- Harvard University
- Boston Children's Hospital
- Genetics Division
- Division of Genetics and Genomics
- Genom. Prog. and Div. of Genetics
- Children's Hospital
- Boston Children's Hospital
External person
Kathryn N. North
- University of Sydney
- Roy. Alexandra Hospital for Children
- The University of Sydney
- Harvard University
- The Children's Hospital at Westmead
- University of Melbourne
- Murdoch Children's Research Institute
- Department of Paediatrics and Child Health
- Neurogenetics Research Unit
- Department of Paediatrics
- Institute for Neuromuscular Research
- Discipline of Paediatrics and Child Health
- Department of Child Health
- Institute for Neuroscience and Muscle Research
- Royal Children's Hospital
- Institute for Neuroscience and Muscle Research
- The Children's Hospital at Westmead
- Boston Children's Hospital
External person
L. Barker
- Cincinnati University Medical Center
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Newington Children's Hospital
- Connecticut Children's Medical Center
- Cincinnati Children's Hospital Medical Center
- Department of Neurology
- Department of Neurology
- Connecticut Children's Medical Center
External person
Jacqueline Montes
- Columbia University
- Departments of Neurology
- Rehabilitation and Regenerative Medicine
- Departments of Rehabilitation and Regenerative Medicine and Neurology
- Departments of Rehabilitative and Regenerative Medicine
- Department of Neurology
- Medical Center
- SMA Clinical Research Center
- The Pediatric Neuromuscular Clinical Research Network
- NYC
External person
K. Burhans
- Cincinnati University Medical Center
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Newington Children's Hospital
- Connecticut Children's Medical Center
- Cincinnati Children's Hospital Medical Center
- Department of Neurology
- Department of Neurology
- Connecticut Children's Medical Center
External person
Wendy M J Bosboom
- Sint Lucas Andreas Hospital
- Utrecht University
- Onze Lieve Vrouwe Gasthuis
- Department of Neurology
- Department of Child Neurology
- Sint Lucas Andreas Hospital
External person
Julaine Florence
- Washington University St. Louis
- Washington University
- University of Washington School of Medicine
- University of Washington
- Department of Neurology
- Department of Neurology
- Spinal Muscular Atrophy Foundation
- Washington University
External person
C. M. Zaidman
- Department of Pediatrics
- Department of Neurology
- Washington University St. Louis
External person
Katherine D. Mathews
- Spinal Muscular Atrophy Foundation
- Division of Neurology
- University of Iowa
- Department of Pediatrics
External person
John H J Wokke
- Sint Lucas Andreas Hospital
- University Medical Centre Utrecht
- Utrecht University
- Department of Neurology
- Onze Lieve Vrouwe Gasthuis
- Department of Neurology
External person
Leonard H. van den Berg
- Sint Lucas Andreas Hospital
- University Medical Centre Utrecht
- Utrecht University
- Department of Neurology
- Onze Lieve Vrouwe Gasthuis
- Department of Neurology
External person
Alexander F J E Vrancken
- Sint Lucas Andreas Hospital
- University Medical Centre Utrecht
- Utrecht University
- Department of Neurology
- Onze Lieve Vrouwe Gasthuis
- Department of Neurology
- Department of Neurology
External person
Elena Mazzone
- Polclinico Gemell, Largo Gemelli
- Policlinico Universitario Agostino Gemelli
- Catholic University of the Sacred Heart
- Paediatric Neurology Unit
- Department of Pediatric Neurology
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- University of Rome La Sapienza
External person
Paula R. Clemens
- Children's Hospital of Pittsburgh
- Baylor College of Medicine
- Department of Veterans Affairs Medical Center
- University of Pittsburgh
- Neurology Service (127)
- VA Medical Center
- Neurology Service
- Department of Veterans Affairs
- Department of Neurology
- Tel Aviv University
External person
Kate Bushby
- Bambino Gesu' Childrens Research Hospital
- Newcastle University
- University of Newcastle Upon Tyne
- University of Newcastle upon Tyne
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Department of Laboratories
- The Institute of Human Genetics
- Institute of Human Genetics
- Institute of Genetic Medicine
- John Walton Muscular Dystrophy Research Centre
- Tel Aviv University
External person
Mary K. Schroth
- University of Wisconsin-Madison
- Division of Pediatric Pulmonary
- Spinal Muscular Atrophy Foundation
External person
Kevin M. Flanigan
- Nationwide Children’s Hospital
- Ohio State University
- Department of Pediatrics
External person
J. E. Heubi
- University of Colorado Denver
- Children's Hospital Medical Center
- University of Cincinnati School of Medicine
- Cincinnati Children's Hospital Medical Center
- Thomas Jefferson University
- University of Cincinnati
- Division of Gastroenterology and Nutrition
- Division of Neurology
- Division of Gastroenterology
- Division of Pathology
- Division of Nutrition
- Departments of Pediatrics and Neurology
- Department of Pediatrics
- Department of Medicine
- Department of Pediatrics
- University of Texas Southwestern Medical Center
- University of Colorado Anschutz Medical Campus
External person
Julie Parsons
- University of Colorado Denver
- University of Colorado Anschutz Medical Campus
- National Jewish Health and University of Colorado
External person
Susan Apkon
- Children's Hospital and Regional Medical Center Seattle
- University of Colorado Denver
- University of Washington
- University of Colorado Anschutz Medical Campus
- Seattle Children's Hospital
External person
C. R. Buncher
- Cincinnati University Medical Center
- Univ. of Cincinnati Medical Center
- University of Cincinnati
- Newington Children's Hospital
- Connecticut Children's Medical Center
- Cincinnati Children's Hospital Medical Center
- Department of Neurology
- Department of Environmental Health
- Department of Epidemiology
- Connecticut Children's Medical Center
External person
Kristin J. Krosschell
- Northwestern University
- Departments of Physical Therapy and Human Movement Sciences and Pediatrics
- Departments of Physical Therapy
- Spinal Muscular Atrophy Foundation
External person
Robert Leshner
- Virginia Commonwealth University
- Children National Medical Center
- Children's Hospital
- Texas Scottish Rite Hosp. Children
- Children's National Medical Center
- Texas Scottish Rite Hospital for Children
- Department of Neurology
- Department of Neurology
- Scottish Rite Hospital for Children
External person
John Day
- University of Minnesota Twin Cities
- Stanford University
- Department of Neurology
- Department of Neurology
External person
T. W. Prior
- Ohio State University
- Ohio State Wexner Medical Center
- Department of Molecular Pathology
- Department of Neurology
- Department of Pathology
External person
E. Bertini
- Bambino Gesu' Childrens Research Hospital
- Laboratory of Molecular Medicine, Bambino Gesù Hospital
- Bambino Gesu' Children's Research Hospital
- Bambin Gesù Children's Hospital
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Unit of Neuromuscular & Neurodegenerative Disorders
- Department of Laboratories
- Department of Neuroscience
- Unit of Molecular Medicine
External person
Tom O. Crawford
- Johns Hopkins Univ. Sch. of Medicine
- Johns Hopkins University
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Neurology and Pediatrics
External person
Richard J. Barohn
- University of Kansas
- University of Texas at Dallas
- Department of Neurology
- Department of Neurology
- Department ofNeurology
- University of Miami
- Department of Neurology
- University of Texas Southwestern Medical Center
- Department of Neurology
- University of Kansas
- Neuromuscular Center
- Presbyterian Hospital of Dallas
- Department of Neurology
- Department of Neurology
- Akron Children's Hospital
- Texas Southwestern Medical Center at Dallas
- University of Kansas
- University of Kansas
- University of Kansas
- Kansas University
- University of Kansas
- Akron Children's Hospital
- Texas Health Presbyterian Hospital Dallas
- University of Kansas
- University of Kansas
- University of Kansas Hospital & Medical Center
- Harvard University
- University of Kansas
- University of Missouri
- University of Missouri
- Children's Mercy Hospitals and Clinics
External person
Brenda L. Wong
- Cincinnati Children's Hospital Medical Center
- Cincinnati Childrens Hospital Medical Center
- Division of Neurology
- Division of Child Neurology
- Division of Pediatric Neurology
- Division of Neurology
- Spinal Muscular Atrophy Foundation
- University of Massachusetts Medical School
- Scottish Rite Hospital for Children
- Texas Scottish Rite Hospital for Children
External person
Már Tulinius
- University of Gothenburg
- Department of Pediatrics
- Sahlgrenska University Hospital
- Department of Pediatrics
- Tel Aviv University
External person
Mathula Thangarajh
- Children's National Medical Center
- Department of Neurology
- Virginia Commonwealth University
External person
H. Topaloǧlu
- Istituto Ortopedico Rizzoli
- Bambino Gesu' Childrens Research Hospital
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Hacettepe University
- Department of Pediatrics
- Division of Pediatric Neurology
- Neuromuscular Unit
- Department of Laboratories
- Hacettepe Children�s Hospital
External person
John T. Kissel
- Ohio State University
- Department of Neurology
- Department of Neurology
- Nationwide Children’s Hospital
- Departments of Neurology and Pediatrics
- Spinal Muscular Atrophy Foundation
- Departments of Neurology and Pediatrics
- Department of Neurology
- Harvard University
External person
B. Perkins
- Cincinnati University Medical Center
- Newington Children's Hospital
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Connecticut Children's Medical Center
- University of Toronto
- Department of Neurology
- Division of Pediatric
- Connecticut Children's Medical Center
- Lunenfeld Tanenbaum Research Institute
- Harvard University
- Sinai Health System
External person
Kristi J. Jones
- Department of Clinical Genetics
- University of Sydney
- Institute for Neuroscience and Muscle Research
- Discipline of Child and Adolescent Health
- Sydney Children's Hospital
- The Children's Hospital at Westmead
External person
M. Farrar
- University of New South Wales
- Sydney Children's Hospital
- Department of Neurology
- School of Women's and Children's Health
- School of Women's and Children's Health
External person
Richard J. Barohn
- University of Kansas
- Univ. Texas Southwestern Med. Sch.
- Children's Hospital Medical Center
- Univ. Texas Southwestern Med. Ctr.
- Presbyterian Hospital of Dallas
- University of Texas at Dallas
- Southwestern Medical School
- S.W. Medical Center
- Univ. Texas Southwestern Med. C.
- University of Kansas Medical School
- Univ. of Texas Health Science Center
- Scottish Rite Hospital
- Kansas University
- University of Texas Southwestern Medical Center
- Southwestern Medical Center
- University of Texas Southwestern Medical Center
- Akron Children's Hospital
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Neuromuscular Center
- Texas Southwestern Medical Center at Dallas
External person
A. Burghes
- Bambino Gesu' Childrens Research Hospital
- Ohio State University
- University of Texas Southwestern Medical Center
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Department of Biological Chemistry & Pharmacology
- Department of Laboratories
- Department of Medical Biochemistry
- Department of Neurology
- Department of Molecular Genetics
- Department of Molecular Genetics
- Department of Neurology
External person
L. Zimmerman
- Cincinnati University Medical Center
- Newington Children's Hospital
- Georgetown University
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Connecticut Children's Medical Center
- Department of Neurology
- Division of Pediatric
- Department of Ophthalmology
- Connecticut Children's Medical Center
External person
Steve Kolb
- Ohio State University
- Department of Neurology
- Department of Biological Chemistry & Pharmacology
- Department of Neurology
- Spinal Muscular Atrophy Foundation
- Department of Neurology
External person
Richard H. Browne
- Univ. Texas Southwestern Med. Ctr.
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. Children
- University of California Office of the President
- University of Texas Southwestern Medical Center
- Texas Scottish Rite Hosp. for C.
- TX Scottish Rite Hosp. for Children
- Texas Scottish Rite Hospital Dallas
- Mayagüez Medical Center
- Texas Scottish Rite Hospital at Dallas
- University of Michigan, Ann Arbor
- Texas Scottish Rite Children Hosp.
- C.V. Starr Hand Center
- N. Kentucky Hand Surgery Specialists
- POASA
- Mayaguez Medical Center
- C.V. Starr Hand Surgery Center
- University of Texas Southwestern Medical Center
- Department of Orthopaedic Surgery
- Departments of Research
- Department of Orthopaedics
- Department of Orthopedic Surgery
- Division of Neonatal-Perinatal Medicine
- Orthotic and Orthopaedic Departments
- Movement Science Laboratory
- Seay Center for Musculoskeletal Research
- Department of Orthopedics
- Center for Excellence in Hip Disorders
- Orthopaedic Department
- Department of Pediatrics
- Department of Neurology
- Department of Anesthesiology and Pain Management
- Pediatric Neurology
- Scottish Rite Hospital for Children
- Seay Center for Musculoskeletal Research
- Department of Orthopaedic Surgery
- Division of Nephrology and Hypertension, Department of Medicine, University of California
- Continuum Health Partners, Inc.
- University of California at Davis
- Division of Project Support Services
- N. Kentucky Hand Surgery Specialists
External person
Gary L. Elfring
- Vanderbilt University
- Pharmacia and Upjohn
- Pfizer
- PTC Therapeutics
- PTC Therapeutics
External person
J. D. Cook
- Newington Children's Hospital
- University of Texas Southwestern Medical Center
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- The University of Texas Health Science Center at Dallas
- Connecticut Children's Medical Center
- Division of Pediatric
- Department of Neurology
- Scottish Rite Hospital for Children
- King Faisal Specialist Hospital and Research Centre
- Department of Veterans Affairs
- VA Medical Center
External person
Stephen Smith
- Hennepin County Medical Center
- Physicians of Hennepin County Medical Center
- Texas Scottish Rite Hosp. Children
- Gillette Children's Specialty Health Care
- Gillette Children's Specialty Healthcare
- Texas Scottish Rite Hospital for Children
- Department of Pathology
- Department of Neurology
- Scottish Rite Hospital for Children
External person
Carina Wallgren-Pettersson
- University of Helsinki
- Univ. Helsinki, Folkhalsan Inst. G.
- Harvard University
- Folkhälsan Dept. of Med. Genet.
- University of Helsinki
- Folkhälsan Inst. of Genetics
- Genetics Division
- Department of Medical Genetics
- Boston Children's Hospital
External person
Sandra Donkervoort
- National Institutes of Health
- National Institutes of Health, Bethesda
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Neurogenetics Branch
External person
Marion Main
- Great Ormond Street Children's Hospital for the Dubowitz Neuromuscular Center
- Great Ormond Street Hospital for Children
- University of Leuven
- University College London
- KU Leuven
- Dubowitz Neuromuscular Centre
- Dubowitz Neuromuscular Centre
- University of Sydney
- Moorfield's Eye Institute of London
- The Children's Hospital at Westmead
- Great Ormond Street Hospital for Children Foundation Trust
External person
Allan M. Glanzman
- Department of Physical Therapy
- Children's Hospital of Philadelphia
- University of Pennsylvania
- Department of Physical Therapy
- Children’s Hospital of Philadelphia
- Department of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- The Pediatric Neuromuscular Clinical Research Network
- Spinal Muscular Atrophy Foundation
- University of Florida
- Department of Physical Therapy
- Departments of Physical Therapy
- The Children's Hospital of Philadelphia
External person
Caroline Sewry
- Hammersmith Hospital
- RJAH Orthopaedic Hospital
- Dubowitz Neuromuscular Centre
- Robert Jones and Agnes Hunt Orthopaedic Hospital
- The Robert Jones and Agnes Hunt Orthopaedic and District Hospital NHS Trust
- Dept. of Paediatr. and Neonatal Med.
- Imperial College London
- Wolfson Centre of Inherited Neuromuscular Diseases
- Centre for Inherited Neuromuscular Disorders
- Department of Paediatrics
- Imperial College Healthcare NHS Trust
- RJAH Orthopaedic Hospital NHS Foundation Trust Oswestry
External person
R. R. Buncher
- Newington Children's Hospital
- Univ. of Cincinnati Medical Center
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Connecticut Children's Medical Center
- Division of Pediatric
- Department of Epidemiology
- Department of Neurology
External person
Anita Simonds
- Royal Brompton Hospital
- NHS Foundation Trust
- NIHR Respiratory Biomedical Research Unit
- National Health Service
- Imperial College London
- Royal Brompton and Harefield NHS Trust
- Moorfield's Eye Institute of London
- Royal Brompton and Harefield NHS Foundation Trust
External person
C. Vogler
- University of Cincinnati Medical Center
- Cincinnati Children's Hospital Medical Center
- University of Cincinnati
- Department of Pathology
External person
T. Gidaro
- Sorbonne Université
- Institut de Myologie
- Institut de Myologie
- Sorbonne Universités
External person
Jahannaz Dastgir
- Columbia University
- Goryeb Children's Hospital
- Goryeb Children's Hospital
- National Institutes of Health
External person
Eugenio Mercuri
- Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- Catholic University of the Sacred Heart
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Imperial College Healthcare NHS Trust
- Hammersmith Hospital
- University of Rome La Sapienza
External person
Kathie M. Bishop
- Ionis Pharmaceuticals
- Ionis Pharmaceuticals
- Columbia University
- Otonomy
- Nemours Children's Clinic
External person
Anna Mayhew
- University of Newcastle
- Newcastle University
- Newcastle Muscle Team
- Newcastle upon Tyne Hospitals NHS Foundation Trust
External person
Jill Mayhew
- Children's Hospital
- Children's Hospital of Virginia
- Texas Scottish Rite Hosp. Children
- Children's Home Society of Virginia
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
Michela Guglieri
- Newcastle University
- Tel Aviv University
- John Walton Muscular Dystrophy Research Centre
- Newcastle upon Tyne Hospitals NHS Foundation Trust
External person
C. Smith
- Cincinnati University Medical Center
- Texas Scottish Rite Hospital for Children
- Newington Children's Hospital
- University of Cincinnati
- Connecticut Children's Medical Center
- Department of Neurology
- Connecticut Children's Medical Center
- Scottish Rite Hospital for Children
External person
Yoram Nevo
- University of Tel Aviv
- Washington Univ. Sch. of Med.
- Tel Aviv University
- Washington University St. Louis
- Department of Neurology
- Hadassah University Medical Centre
External person
Michelle Eagle
- Newcastle University
- The Institute of Human Genetics
- Institute of Genetic Medicine
- ATOM International Ltd
External person
Alan Pestronk
- Washington University St. Louis
- Washington Univ. School of Medicine
- Box 8096
- Johns Hopkins University
- Washington University School of Medicine
- Washington Univ. Sch. of Med.
- Ophthalmology/Visual Science Dept.
- Rush Presbyterian Medical Center
- Washington University
- University of Washington
- Rush University
- Department of Neurology
- Department of Pathology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Departments of Pathology and Immunology (CC
- Neurology/Neurosurgery Intensive Care Unit
- Department of Pathology and Immunology
- Dept. of Ophthalmol./Visual Sciences
- Washington University
- Box 8096
- University of Pennsylvania
- Oregon Health and Science University
External person
Susana Quijano-Roy
- APHP Raymond Poincare University Hospital (UVSQ)
- Hôpital Raymond Poincaré
- Hôpital Raymond Poincaré
- Institut national de la santé et de la recherche médicale
- Department of Pediatrics
- ComUE Paris-Saclay
External person
Tulio Bertorini
- University of Tennessee Health Science Center
- University of Tennessee, Knoxville
- Wesley Neurology Clinic
External person
Kristy Rose
- The Children's Hospital at Westmead
- University of Sydney
- Institute for Neuroscience and Muscle Research
- University of Pennsylvania
- The Children's Hospital at Westmead
- The Children's Hospital of Philadelphia
External person
W. F. Balistreri
- Thomas Jefferson University
- Cincinnati Children's Hospital Medical Center
- Department of Medicine
- University of Colorado Denver
- University of Cincinnati
- Department of Pediatrics
- University of Colorado Anschutz Medical Campus
- Division of Gastroenterology
- Akron Children's Hospital
- Hepatology
- Akron Children's Hospital
External person
Corinne D. Strickland
- Harvard University
- Children's Hospital
- Genetics Division
- Genom. Prog. and Div. of Genetics
- Boston Children's Hospital
External person
Kathryn Selby
- University of British Columbia
- University of British Columbia
- Department of Pediatrics
- Child and Family Research Institute, Canada
External person
E. Tizzano
- Bambino Gesu' Childrens Research Hospital
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Autonomous University of Barcelona
- Department of Clinical and Molecular Genetics
- Department of Laboratories
- Hospital Universitari Vall d'Hebron
External person
Heather Gordish-Dressman
- Children's National Health System/The George Washington University School of Medicine and Health Sciences
- Children's National Medical Center
- Tel Aviv University
- Children's National Hospital
External person
Sandra P. Reyna
- University of Utah
- Harvard University
- Biogen IDEC
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Neurology
- Department of Pediatrics
- Massachusetts General Hospital
External person
Katarina Pelin
- University of Helsinki
- Univ. Helsinki, Folkhalsan Inst. G.
- University of Helsinki
- Folkhälsan Inst. of Genetics
- Department of Biological and Environmental Sciences
External person
K. R. Chao
- Broad Institute
- Massachusetts Institute of Technology
- Analytic and Translational Genetics Unit
- Harvard University
- Program in Medical and Population Genetics
- Massachusetts General Hospital
External person
Lindsay N. Alfano
- Department of Pediatrics
- Ohio State University
- Nationwide Children’s Hospital
External person
Giacomo P. Comi
- University of Milan
- IRCCS Fondazione Ca'Granda – Ospedale Maggiore Policlinico - Milano
- Neurology Unit
External person
I. A. Khatri
- Texas Scottish Rite Hosp. Children
- Shifa International Hospital
- Texas Scottish Rite Hospital for Children
- Department of Neurology
- Department of Neurology
- Division of Neurology
- Scottish Rite Hospital for Children
- Shifa International Hospital
External person
C. Siener
- Department of Neurology
- Washington University St. Louis
- Spinal Muscular Atrophy Foundation
- Tel Aviv University
- TRiNDS LLC
External person
Andrew J. Kornberg
- Murdoch Children's Research Institute
- Washington University St. Louis
- Royal Children's Hospital
- Neurosciences Department
- Department of Neurology
External person
Ai Sakonju
- University of Utah
- SUNY Upstate Medical University
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Pediatrics
External person
K. Harris
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. Children
- Department of Respiratory Therapy
- Scottish Rite Hospital for Children
External person
Hollis Owens
- Department of Physical Therapy
- Texas Scottish Rite Hosp. Children
- Texas Scottish Rite Hospital for Children
- Department of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- Department of Physical Therapy
- Scottish Rite Hospital for Children
External person
J. Ben Renfroe
- Child Neurology Center of Northwest Florida
- Northwest Florida Clinical Research Group
External person
Jennifer M. Kwon
- Washington Univ. School of Medicine
- Washington University St. Louis
- Department of Neurology
- Department of Surgery
- Temple University
- Department of Neurology
- University of Wisconsin-Madison
- Duke University
External person
Petra Kaufmann
- Departments of Neurology
- Columbia University
- Columbia University
- Neurologic Institute
- Department of Neurology
- Eleanor and Lou Gehrig MDA/ALS Research Center
- Department of Neurology
- SMA Clinical Research Center
- The Pediatric Neuromuscular Clinical Research Network
- Department of Neurology
- Université Grenoble Alpes
- Department of Neurology
- Center for Brain Health
- Department of Neurology
External person
M. Hovmöller
- Astrid Lindgren Children Hospital
- Astrid Lindgren Children Hospital
- Karolinska Institutet
External person
Laurent Servais
- Institute of Motion
- Division of Endocrinology and Diabetes
- University of Oxford
- Medical Sciences Division
- University of Liege
External person
A. R. Foley
- National Institutes of Health
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- The Pediatric Neuromuscular Clinical Research Network
- Dubowitz Neuromuscular Centre
- University College London
- Neuromuscular and Neurogenetic Disorders of Childhood Section
External person
B. Estournet-Mathiaud
- Istituto Ortopedico Rizzoli
- Bambino Gesu' Childrens Research Hospital
- Hôpital Raymond Poincaré
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Hôpital Raymond Poincaré
- Neuromuscular Unit
- Department of Laboratories
External person
K. Zilke
- Texas Scottish Rite Hosp. Children
- Shriners Hospital for Children
- Shriners Hospitals for Children
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
Diana M. Escolar
- Children's National Medical Center
- George Washington University
- Department of Neurology and Pediatrics
External person
Gil I. Wolfe
- Univ. Texas Southwestern Med. Ctr.
- Veterans Affairs Medical Center
- Univ. Texas Southwestern Med. Sch.
- University of Texas at Dallas
- University of Texas Southwestern Medical Center
- Women and Children's Hospital of Buffalo
- Univ. of TX Southwestern Med. Center
- Southwestern Medical School
- Buffalo School of Medicine and Biomedical Sciences
- Department of Neurology
- Univ. Texas Southwestern Med. C.
- State University of New York at Buffalo
- Univ. of Texas Health Science Center
- Dept. Int. Med.; Div. N.
- Scottish Rite Hospital
- Southwestern Medical Center
- University of Texas Southwestern Medical Center at Dallas
- University of Buffalo
- University of Texas Southwestern Medical Center
- SUNY Buffalo
- Div. N
- VA Medical Center
- Univ. of TX Southwestern Med. Center
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Divisions of Epidemiology
- Texas Southwestern Medical Center at Dallas
- Department ofNeurology
- University of Miami
External person
P. H. Buschang
- Baylor College of Medicine
- Seay Center for Musculoskeletal Res.
- Texas Scottish Rite Hospital for Children
- University of Texas Southwestern Medical Center
- University of Texas at Dallas
- Department of Orthodontics
- Seay Center for Musculoskeletal Research
- Texas A&M University
- Department of Radiology (C.M.M.
- Scottish Rite Hospital for Children
External person
Robert J. Graham
- Harvard University
- Division of Critical Care
- Division of Critical Care Medicine
- Boston Children's Hospital
External person
D. M. Sproule
- Departments of Neurology, Physiology, and Pediatrics
- The Pediatric Neuromuscular Clinical Research Network
- Novartis Gene Therapies
External person
O. Mayer
- University of Pennsylvania
- Division of Pulmonology
- Children's Spine Foundation
- The Children's Hospital of Philadelphia
External person
Juan J. Vilchez
- University of Valencia
- Hospital Universitario La Fe
- Hospital Quirónsalud Valencia
External person
B. L. Wong
- Cincinnati Children's Hospital Medical Center
- Texas Scottish Rite Hosp. Children
- Texas Scottish Rite Hospital for Children
External person
Anne Rutkowski
- Kaiser SCPMG
- Cure CMD
- S.C.P.M.G.
- Kaiser Permanente
- University of California at Los Angeles
- California Poison Control System
- Cure Congenital Muscular Dystrophy (Cure CMD)
- Cure CMD
- Goryeb Children's Hospital
External person
Kayoko Saito
- Institute of Medical Genetics
- Tokyo Women's Medical University
- Institute of Medical Genetics and Department of Pediatrics
External person
Diana X. Bharucha-Goebel
- Children's National Medical Center
- National Institutes of Health, Bethesda
- Division of Neurology
- National Institutes of Health
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Neuromuscular and Neurogenetic Disorders of Childhood Section
External person
N. Butler-Simon
- University of Colorado Denver
- Department of Pediatrics
- Cincinnati Children's Hospital Medical Center
- University of Colorado Anschutz Medical Campus
External person
Michelle M. Mcgovern
- Harvard University
- Harvard Partners
- Department of Neurology
- Department of Neurology
- Massachusetts General Hospital
External person
N. Joyce
- University of California at Davis
- University of California Office of the President
- Harvard University
External person
A. Silverman
- University of Colorado Denver
- Cincinnati Children's Hospital Medical Center
- University of Cincinnati
- University of Colorado Anschutz Medical Campus
External person
William D. Arnold
- Ohio State University
- Department of Neurology
- Department of Physical Medicine and Rehabilitation
- Department of Neurology
- University of Washington
External person
S. Gheuens
- Harvard University
- Division of Viral Pathogenesis
- Biogen IDEC
- Division of NeuroVirology
- Department of Neurology
- Columbia University
- Massachusetts General Hospital
External person
Kati Donner
- University of Helsinki
- Univ. Helsinki, Folkhalsan Inst. G.
- University of Helsinki
- Folkhälsan Inst. of Genetics
External person
Robert C. Griggs
- University of Rochester
- Univ. Texas Southwestern Med. Ctr.
- University of Rochester Medical Centre
- University of Texas Southwestern Medical Center
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Archives of Neurology.
- Neurology
- Neurology
- Department of Neurology
External person
V. Doppler
- Sorbonne Université
- Institut de Myologie
- Institut de Myologie
- Sorbonne Universités
External person
Jay D. Cook
- Texas Scottish Rite Hospital for Children
- Alfaisal University
- Department of Pediatrics
- Scottish Rite Hospital for Children
- King Faisal Specialist Hospital and Research Centre
External person
B. Wirth
- Bambino Gesu' Childrens Research Hospital
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Center for Molecular Medicine CologneCologne
- Center for Molecular Medicine Cologne
- Institute of Human Genetics
- University of Cologne
- Department of Laboratories
- Institute of Human Genetics
External person
Anne A. Morton
- Department of Psychology
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. Children
- Department of Psychology
- Department of Orthopaedic Surgery
- University of Texas Southwestern Medical Center
- Scottish Rite Hospital for Children
- Department of Orthopedics
- Department of Orthopaedic Surgery
External person
Günther Bernert
- G. v. Preyer'sches Kinderspital
- IRCCS Istituto Eugenio Medea - Bosisio Parini (LC)
External person
Betsy Perkins
- Connecticut Children's Medical Center
- Connecticut Children's Medical Center
External person
Paolo Spagnolo
- Santhera Pharmaceuticals
- Santhera Pharmaceuticals
- University of Padua
- Clinica di Malattie dell'Apparato Respiratorio
External person
Christopher S. Coffey
- Department of Biostatistics
- University of Iowa
- University of Pittsburgh
- University of Alabama at Birmingham
- Banner Health
External person
Laurie Zimmerman
- Connecticut Children's Medical Center
- Connecticut Children's Medical Center
External person
Linda Lowes
- Department of Pediatrics
- Ohio State University
- Nationwide Children’s Hospital
External person
Kathryn North
- Institute for Neuroscience and Muscle Research
- Royal Children's Hospital
- University of Sydney
External person
Isabelle Desguerre
- Hôpital Saint-Vincent-de-Paul
- Hôpital Saint Vincent de Paul
- Paris Descartes University, Sorbonne Paris Cité, Necker Medicine Faculty
- Université Paris Cité
- Université Paris 5
External person
C. McLaughlin
- Texas Scottish Rite Hospital for Children
- University of Cincinnati
- Scottish Rite Hospital for Children
External person
R. C. Richardson
- Children's Hospital and Regional Medical Center Seattle
- Nemours Children's Clinic
External person
Carole Vuillerot
- Woman-Mother-Child Hospital (HFME)
- Universite Claude Bernard Lyon 1
- Cure CMD
- Hospices Civils de Lyon
- Universite de Lyon
External person
Timothy Lotze
- Baylor College of Medicine
- Child Neurology
- Department of Child Neurology
- Division of Pediatric Neurology
- Division of Pediatric Neurology
- Blue Bird Circle Multiple Sclerosis Center
- Department of Neurology
- Division of Infectious Diseases
- Division of Child Neurology
- The Blue Bird Circle Clinic for Multiple Sclerosis
- Neurology and Developmental Neuroscience Department
- Texas Children's Hospital Houston
- University of Texas Southwestern Medical Center
External person
J. Perrault
- University of Colorado Denver
- Mayo Clinic Rochester, MN
- Department of Pediatrics
- Department of Pediatrics
External person
Wilson W. Bryan
- Univ. Texas Southwestern Med. Ctr.
- Veterans Affairs Medical Center
- Univ. Texas Southwestern Med. Sch.
- University of Texas at Dallas
- Biologics Consulting Group Inc.
- Southwestern Medical School
- S.W. Medical Center
- Univ. of Texas Health Science Center
- Dept. Int. Med.; Div. N.
- University of Texas at Austin
- University of Texas Southwestern Medical Center at Dallas
- University of Texas Southwestern Medical Center
- University of Texas Southwestern Medical Center
- Div. N
- VA Medical Center
- Department of Neurology
- Divisions of Epidemiology
- Texas Southwestern Medical Center at Dallas
External person
Jong Hee Chae
External person
Ching H. Wang
- Stanford University
- Department of Neurology
- Spinal Muscular Atrophy Foundation
- Driscoll Children's Hospital
- Departments of Neurology and Pediatrics
- Department of Neurology
External person
Payam Mohassel
- National Institutes of Health
- Neurogenetics Branch
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Neuromuscular and Neurogenetic Disorders of Childhood Section
External person
Victor Dubowitz
- Hammersmith Hospital
- Imperial College London
- Imperial College Healthcare NHS Trust
- Moorfield's Eye Institute of London
External person
Jonathan Marra
- Columbia University
- SMA Clinical Research Center
- The Pediatric Neuromuscular Clinical Research Network
External person
M. A. Guggenheim
- University of Colorado Denver
- Cincinnati Children's Hospital Medical Center
- University of Cincinnati
- General Clinical Research Center
- University of Colorado Anschutz Medical Campus
External person
Robert Miller
- California Pacific Medical Center
- University of Toronto
- Department of Neurosciences
- Forbes Norris ALS Center
- Department of Neurology
- Toronto Hospital
External person
Lloyd K. Shield
- Royal Children's Hospital
- Royal Children's Hospital
- Department of Neurology
- Department of Neurology
- Department of Neurology
External person
J. Melki
- Istituto Ortopedico Rizzoli
- Bambino Gesu' Childrens Research Hospital
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- IRCCS Ospedale pediatrico Bambino Gesù - Roma
- Neuromuscular Unit
- Department of Laboratories
- Assistance publique – Hôpitaux de Paris
- GENOPOLE
External person
Heather R. Gilbreath
- Department of Advanced Practice, Children's Medical Center of Dallas
- Children's Medical Center Dallas
- Department of Advanced Practice Services
- Children's Medical Center Dallas
External person
Leslie A. Morrison
- University of New Mexico
- Department of Neurology
- Department of Neurology
External person
Erik Jan Kamsteeg
- Radboud University Nijmegen
- Department of Human Genetics
- Donders Institute for Brain
External person
Oscar H. Meyer
- University of Pennsylvania
- Division of Pulmonology
- The Children's Hospital of Philadelphia
External person
David Birnkrant
- MetroHealth Medical Center Cleveland
- Case Western Reserve University
- Department of Pediatrics
External person
Hans H. Goebel
- Johannes Gutenberg University
- Johannes Gutenberg University Mainz
- Department of Neuropathology
External person
Brenda L. Wong
- University of Massachusetts Medical School
- Cincinnati Children's Hospital Medical Center
External person
M. Heyman
- University of Colorado Denver
- San Francisco School of Medicine
- University of California at San Francisco
- University of California at San Francisco
- University of California Office of the President
- University of Pittsburgh
- Cincinnati Children's Hopsital Medical Center
- Division of Pediatric Gastroenterology
- Department of Pediatrics
- Division of Adolescent and Young Adult Medicine
- Department of Pediatrics
- Departments of Pediatrics and Neurology
- Pediatric Gastroenterology
- University of Washington
- Seattle Children's Hospital
External person
George Benzing
- University of Cincinnati
- Cincinnati Children's Hospital Medical Center
- Department of Pediatrics
External person
Wendy King
- Ohio State University
- Department of Neurology
- Spinal Muscular Atrophy Foundation
External person
Deborah Gelinas
- Nashoba Valley Healthcare Group
- California Pacific Medical Center
- Department of Neurology
External person
Jeremy M. Shefner
- SUNY - Upstate Medical University
- SUNY Albany
- SUNY Upstate Medical University
- St. Joseph's Hospital and Medical Center, Phoenix
- Department of Neurology
- Department of Neurology
- Columbia University
- State University of New York System
- University of Arizona
- Creighton University
External person
Carla Grosmann
- Rady Children's Hospital
- Department of Neurology
- University of California at San Diego
External person
Michelle Mendoza
- California Pacific Medical Center
- Forbes Norris ALS Center
- Department of Neurology
External person
Rhonda Newman
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
K. Rabb
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. Children
- Scottish Rite Hospital for Children
External person
Janet Smith
- University of Texas Southwestern Medical Center
- Texas Scottish Rite Hosp. Children
- Texas Scottish Rite Hospital for Children
- University of Texas Southwestern Medical Center
- Department of Clinical Sciences
External person
Lindsay C. Swanson
- Boston Children's Hospital
- Harvard University
- Division of Genetics and Genomics
- Translational Neuroscience Center
- Boston Children's Hospital
External person
Cristian Ionita
- University of Arkansas for Medical Sciences
- Neuromuscular Diagnostic Clinic
- University of Arkansas for Medical Sciences
External person
Pankaj B. Agrawal
- Boston Children's Hospital
- Harvard University
- Division of Genetics and Genomics
- Division of Newborn Medicine
- Division of Neonatology
- Genom. Prog. and Div. of Genetics
- Children's Hospital
- Boston Children's Hospital and Harvard Medical School
- Boston Children's Hospital
External person
Darryl C. De Vivo
- Colleen Giblin Research Laboratories for Pediatric Neurology Columbia University
- Columbia University
- Neurological Institute
- College of Physicians Surgeons
- Columbia University
- Colleen Giblin Foundation
- Departments of Neurology and Pediatrics
- Department of Neurology
- Department of Pediatrics
- Department of Neurology
- Department of Pediatrics
- Center for Brain Health
- Department of Pediatrics
- College of Physicians and Surgeons
- Department of Physiology and Cellular Biophysics
- Dept. of Physiology
- Department of Neurology
- Colleen Giblin Laboratories
- Department of Pediatrics
- Department of Neurology
- The Pediatric Neuromuscular Clinical Research Network
- Department of Neurology
- Department of Neurology
External person
Vicki L. Mcgovern
- Ohio State University
- Department of Biological Chemistry & Pharmacology
External person
D. Villano
External person
A. Harper
- Virginia Commonwealth University
- Department of Neurology
- Carolinas Medical Center
- Children's Hospital of Richmond
External person
Cindy Smith
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
Merit Cudkowicz
- Harvard University
- Harvard Partners
- Department of Neurology
- Department of Neurology
- Neurological Clinical Research Institute (NCRI)
- Department of Neurology
- Department of Neurology
- Massachusetts General Hospital
External person
J. Stout
- Texas Scottish Rite Hosp. Children
- Gillette Children's Specialty Health Care
- Gillette Children's Specialty Healthcare
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
Brian S. Tseng
- Univ. Texas M. D. Anderson Cancer C.
- Univ. of Texas at Houston Med. Sch.
- University of Colorado Denver
- Harvard University
- University of Texas MD Anderson Cancer Center
- University of Texas Health Science Center at Houston
- Hamon Ctr Bas.Canc.Res.
- Department of Biochemistry and Molecular Biology
- Department of Integrative Biology
- Department of Neurology
- Dept. of Molec. Biol. and Oncol.
- Department of Molecular Pathology
- Department of Pediatrics
- University of Texas Southwestern Medical Center
- Molecular Biology and Oncology
- Department of Molecular Pathology
- University of Colorado Anschutz Medical Campus
- Massachusetts General Hospital
External person
Richard T. Abresch
- UC Davis Children's Hospital
- University of California at Davis
- Critical Path Institute
- Critical Path Institute
External person
F. Sinatra
- University of Colorado Denver
- University of Southern California School of Medicine
- University of Southern California
- Department of Pediatrics
- Department of Pediatrics
- Children's Hospital Los Angeles
External person
Edward M. Kaye
- Genzyme Corporation
- Sarepta Therapeutics
- University of Pennsylvania
- Department of Pediatrics
- Sarepta Therapeutics
External person
Kevin A. Strauss
- Clinic for Special Children
- Lancaster General Hospital
- University of Massachusetts Medical School
External person
P. T. Golumbek
- Department of Pediatrics
- Department of Neurology
- Washington University St. Louis
External person
Hugh J. McMillan
- Children's Hospital of Eastern Ontario
- Centre hospitalier pour enfants de l'est de l'Ontario
- Department of Neurology
- McGill University
- University of Ottawa
- McGill University
External person
K. L. De Valle
External person
Matthew Wicklund
- Pennsylvania State University
- University of Colorado Denver
- University of Colorado Anschutz Medical Campus
- Pennsylvania State University Hershey
- University of Texas Health Science Center at San Antonio
External person
S. H. Subramony
- University of Mississippi
- Department of Neurology
- University of New Mexico
- University of Florida
- Emory University
External person
D. Muirhead
- UT Southwestern Medical Center
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
A. K. Kroksmark
External person
A. Fritch
- Cincinnati Children's Hospital Medical Center
- Texas Scottish Rite Hosp. Children
- Texas Scottish Rite Hospital for Children
- Scottish Rite Hospital for Children
External person
Peter J. Keebler
- University of Cincinnati
- Cincinnati Children's Hospital Medical Center
- Department of Physical Medicine and Rehabilitation
External person
Henk Granzier
- University of Arizona
- Washington State University Pullman
- Department of Physiology
- Department of Veterinary
- Department of Cellular and Molecular Medicine
External person
J. Levy
- University of Colorado Denver
- Cornell University Medical College
- New York University
- Cornell University
- Department of Pediatrics
- Columbia University
- Department of Pediatrics
- College of Physicians and Surgeons
External person
Beryl B. Cummings
- Massachusetts Institute of Technology
- Analytic and Translational Genetics Unit
- Harvard University
- Program in Biological and Biomedical Sciences
- Broad Institute
- Program in Medical and Population Genetics
- Janssen
- Massachusetts General Hospital
External person
Volker Straub
- University of Iowa College of Medicine
- University of Iowa
- Dept. of Physiology and Biophysics
- Newcastle University
- John Walton Muscular Dystrophy Research Centre
- NHS Foundation Trust
- National Health Service
- Newcastle upon Tyne Hospitals NHS Foundation Trust
External person
L. Merlini
- Istituto Ortopedico Rizzoli
- IRCCS Istituto Ortopedico Rizzoli - Bologna
- Neuromuscular Unit
- Istituto Ortopedico Rizzoli IOR-IRCCS
External person
K. M. Carroll
External person
A. Murphy
External person
Georgios Manousakis
- University of Wisconsin-Madison
- Department of Neurology
- University of Minnesota Twin Cities
External person
Anne M. Connolly
- Washington University St. Louis
- Hôpital Universitaire des Enfants Reine Fabiola
- Queen Fabiola Children's University Hospital
External person
Ana Ferreiro
- Groupe Hospitalier Pitié-Salpêtrière
- UMR 787 Groupe Myologie
- Sorbonne Université
- Pathophysiology of Striated Muscles Laboratory
- Université Paris 7
- Public Hospital Network of Paris
- Paris Diderot University/CNRS
External person
James W. Varni
- Texas AandM University
- Texas A&M University
- Department of Pediatrics, College of Medicine, Texas A and M University
- Texas A&M University
- College of Architecture, Texas A and M University, College Station
- Department of Pediatrics
- Department of Landscape Architecture and Urban Planning
- Department of Pediatrics
External person
Christine A. Limbers
- Texas A&M University
- Baylor University
- Department of Psychology
- Dept. of Psychology and Neuroscience
External person
Christina Schnell
- Children's Hospital at Westmead (Royal Alexandra Hospital for Children)
- Roy. Alexandra Hospital for Children
- University of Sydney
- Neurogenetics Research Unit
- The Children's Hospital at Westmead
External person
Medrith Greene
- Children's Medical Center Dallas
- University of Texas Southwestern Medical Center
- Department of Research
- Children's Medical Center Dallas
External person
James R. Lupski
- Baylor College of Medicine
- Department of Molecular and Human Genetics
- Division of Infectious Diseases
- Institute for Molecular Genetics
- Human Genome Sequencing Center
- Department of Pediatrics
- Texas Children's Hospital
- Department of Molecular and Human Genetics
- Texas Children's Cancer Center
- Dept. of Molec. and Human Genetics
- Medical Genetics Laboratory
- Department of Molecular and Human Genetics
- Human Genome Sequencing Center
- Department of Molecular and Human Genetics
- Department of Molecular and Human Genetics
- Baylor-Hopkins Center for Mendelian Genomics of the Department of Molecular and Human Genetics
- Institute for Molecular Genetics
- Human Genome Center
- Medical Genetics Laboratories
- Department of Pediatrics
- Texas Children's Hospital Houston
- BCM
External person
D. C. De Vivo
- Departments of Neurology
- Columbia University
- Department of Neurology
- Neurologic Institute
- SMA Clinical Research Center
- Department of Pediatric Neurology
- SMA Clinical Research Center
External person
Sally Dunaway
- Columbia University
- SMA Clinical Research Center
- The Pediatric Neuromuscular Clinical Research Network
External person
M. Oskoui
- Departments of Neurology, Physiology, and Pediatrics
- McGill University
- Columbia University
- Department of Neurology
- The Pediatric Neuromuscular Clinical Research Network
- Department of Neurology
External person
C. Midgett
- Harvard University
- Children's Hospital
- Genetics Division
- Genom. Prog. and Div. of Genetics
- Boston Children's Hospital
External person
Steven A. Moore
- University of Iowa
- Department of Pathology
- Department of Pathology
- Department of Pathology
- Department of Pathology
- Fort Sanders Regional Medical Center
External person
Duangrurdee Wattanasirichaigoon
- Harvard University
- Genetics Division
- Boston Children's Hospital
External person
S. T. Iannaccone
- Texas Scottish Rite Hospital for Children
- University of Texas Southwestern Medical Center
- University of Texas at Dallas
- Department of Pediatric Surgery
- Children's Medical Center Dallas
- Spinal Muscular Atrophy Foundation
- Department of Pediatrics and Neurology
- Scottish Rite Hospital for Children
- Children's Medical Center Dallas
External person
N. Deconinck
- Department of Pediatric Neurology
- Queen Fabiola Children's University Hospital
- Ghent University
External person
V. Battista
- Departments of Neurology
- Columbia University
- Boston College
- Neurologic Institute
- Department of Neurology
- SMA Clinical Research Center
- The Pediatric Neuromuscular Clinical Research Network
- Department of Neurology
- Department of Neurology
External person
Samantha R. Renusch
- Ohio State University
- Department of Biological Chemistry & Pharmacology
External person
N. S. Seale
- Baylor College of Medicine
- Scottish Rite Hospital for Children
- Texas A&M University
- Texas Scottish Rite Hospital for Children
External person
Tina Duong
- Children's National Medical Center
- Stanford University
- Cincinnati Children's Hospital Medical Center
- Johns Hopkins University
External person
John J. Buchino
- University of Louisville
- Norton's Children's Hospital
- Kosair Children's Hospital
- Kosair Charities Pediatric Clinical Research Unit
- Department of Pathology
- Department of Pathology
External person
Merit E. Cudkowicz
- Harvard University
- Department of Neurology
- Department of Neurology
- Neurological Clinical Research Institute (NCRI)
- Massachusetts General Hospital
External person
D. Carman
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. Children
- Scottish Rite Hospital for Children
External person
C. Miller
External person
Michael W. Lawlor
- Medical College of Wisconsin
- Department of Pathology and Laboratory Medicine
External person
J. C. Webster
- Texas Scottish Rite Hosp. Children
- Texas Scottish Rite Hospital for Children
- University of Texas Southwestern Medical Center
- Academic Computing Services
- Scottish Rite Hospital for Children
External person
Seward Rutkove
- Harvard University
- Department of Neurology
- Department of Neurology
- Beth Israel Deaconess Medical Center
External person
Lisa L. Shockley
- University of Cincinnati
- Cincinnati Children's Hospital Medical Center
- Department of Pediatrics
External person
Albert de la Chapelle
- Department of Medical Genetics University of Helsinki
- University of Helsinki
- Johns Hopkins University
- Johns Hopkins Oncology Center
- Ohio State University
- University of Helsinki
- Human Cancer Genetics Program
- Folkhälsan Inst. of Genetics
- Folkhälsan Institute of Genetics
External person
Molly Snyder
- Department of Neurology
- University of Texas Southwestern Medical Center
- Children's Health
- Children's Health
External person
S. Sakamuri
External person
W. R. Markesbery
- University of Rochester
- University of Kentucky
- Sanders-Brown Center on Aging
- Departments of Pathology and Neurology
- Department of Pathology and Laboratory Medicine
External person
M. Bertoli
External person
H. Verhelst
External person
A. Pechmann
External person
Anthony A. Amato
- Harvard University
- Veterans Affairs Medical Center
- Univ. of Texas Health Science Center
- Univ. of Texas Hlth. Sciences Center
- Univ. Texas Hlth. Sci. Ctr. S. A.
- University of Texas Health Science Center at San Antonio
- VA Medical Center
- Department of Neurology
- Department of Neurology
- Division of Clinical Immunology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Department of Neurology
- Division of Cognitive and Behavioral Neurology
- Brigham and Women’s Hospital
- Massachusetts General Hospital
- University of Texas Health Science Center
External person
C. M. Harper
- Mayo Clinic Rochester, MN
- Division of Neurogenetics
- Department of Neurology
- Department of Neurology
External person
Peter B. Kang
External person
L. Johnson
- University of California at Davis
- Department of Physical Medicine and Rehabilitation
External person
V. Allen
External person
Carlo Minetti
- Istituto Gaslini
- Thomas Jefferson University
- G. Gaslini Institute
- Gaslini Institute
- G. Gaslini Pediatric Institute
- University of Genoa
- IRCCS Istituto Giannina Gaslini - Genova
- Servizio Malattie Neuro-Muscolari
- Department of Radiation Oncology and Cancer Biology
- Muscular and Neurodegenerative Disease Unit
- Unit of Muscular and Neurodegenerative Disease
External person
J. D. Endsley
External person
P. J. Morehart
- Cincinnati Children's Hospital Medical Center
- Spinal Muscular Atrophy Foundation
External person
Paola Melacini
- Department of Cardiac, Thoracic, and Vascular Sciences, Department of Cardiology
- University of Padua
- University of Padua
External person
K. Gwinn-Hardy
- National Institutes of Health
- Mayo Clinic Jacksonville
- Mayo Clinic Jacksonville, FL
External person
Clemens R. Müller
- University of Würzburg
- University of Würzburg
- Department of Human Genetics
External person
Catherine Sy
- The Children's Hospital at Westmead
- University of Sydney
- Western Sydney Genetics Program
External person
Conrad P. Earnest
- LSU Pennington Biomedical Research Center
- Data and Safety Monitoring Committee
- Texas A&M University
- University of Texas Southwestern Medical Center
- Department for Health and Kinesiology
- Texas Woman's University
- Department of Kinesiology
External person
E. D. Austin
External person
Scott Demarest
- University of Colorado Anschutz Medical Campus
- University of Colorado Denver
- The Children's Hospital, Aurora
- National Jewish Health and University of Colorado
External person
T. Kandula
External person
S. Richards
- Baylor College of Medicine
- The University of Texas Health Science Center
- University of Texas Health Science Center
- Department of Biochemistry
- University of Texas Southwestern Medical Center
- Institute for Molecular Genetics
- Department of Biochemistry
- VA Medical Center
- Department of Neurology
- VA North Texas Health Care System
- Department of Microbiology
- Howard Hughes Medical Institute and Department of Neuroscience
External person
Agnes Rotig
- Hôpital Necker-Enfants Malades
- Université René Descartes
- Université Paris 5
- Department of Genetics
- Institut national de la santé et de la recherche médicale
- Université Paris Cité
- Paris Descartes University, Sorbonne Paris Cité, Necker Medicine Faculty
External person
L. Smith
External person
Salla Ranta
- University of Helsinki
- University of Helsinki
- Department of Biological and Environmental Sciences
External person
H. L. Teoh
External person
Stephanie Burns-Wechsler
External person
Navil Sethna
- Harvard University
- Department of Anesthesiology
- Division of Critical Care
- Boston Children's Hospital
External person
W. Leon
External person
C. Wood
External person
T. N. Shun
External person
L. Lucarini
- University of Florence
- University of Florence
- Department of Medical and Surgical Critical Care-Unit of Human Pathology
External person
H. Lee Sweeney
External person
F. Al-Ghamdi
External person
M. del Mar Garcia Romero
External person
J. Taytard
External person
A. G. Engel
- Mayo Clinic Rochester, MN
- Division of Neurogenetics
- Department of Neurology
- Department of Neurology
External person
Agnes Delahodde
- Univ. of TX Southwestern Med. Ctr.
- University of Texas Southwestern Medical Center
- Department of Internal Medicine
- Université Paris-Saclay
- Universite Paris Saclay
External person
S. So
External person
S. Ito
External person
Albert Fujak
- Friedrich-Alexander-University Erlangen-Nuremberg
- Friedrich-Alexander University Erlangen-Nürnberg
External person
P. Uapinyoying
- National Institutes of Health
- Neuromuscular and Neurogenetic Disorders of Childhood Section
- Children's National Medical Center
External person
C. Johnson
External person
Martin Tristani-Firouzi
- University of Utah
- Department of Pediatrics
- Department of Pediatrics
External person
John Vissing
- National University Hospital
- University of Copenhagen
- University of Copenhagen
- KAS Gentofte
- IEEM
- University Hosp. of Copenhagen
- Copenhagen Muscle Research Center
- University of Texas Southwestern Medical Center
- Rigshospitalet
- Danish Multiple Sclerosis Center
- Department of Neurology
- Copenhagen Muscle Res. Center
- Department of Neurology 2082
- Dept. of Neurology
- Neuromuscular Center
- Department of Neurology
- Department of Neurology
- Department of Neurology 2082
- Department of Neurology
- Neuromuscular Clinic
- Dept. of Neurology
- Copenhagen Muscle Research Center, Rigshospitalet
- Neuromuscular Research Unit 3342
- Department of Medical Physiology
- Copenhagen Neuromuscular Center
- Columbia University
- Akron Children's Hospital
- Harvard University
- Akron Children's Hospital
- University of Texas at Dallas
- Chinese University of Hong Kong
- University of Pittsburgh
- National University Hospital
External person
PH Lister
External person
Tracy A. Glauser
- Cincinnati Children's Hospital Medical Center
- Department of Neurology
- University of Cincinnati
External person
O. T. Yilmaz
External person
Ted Abresch
External person
F. Trucco
External person
M. Toms
External person
Daniel G. MacArthur
- Wellcome Research Laboratories, London
- Harvard University
- Wellcome Sanger Institute
- Broad Institute
- Analytic and Translational Genetics Unit
- Medical and Population Genetics Program
- Massachusetts Institute of Technology
- Program in Medical and Population Genetics
- Massachusetts General Hospital
External person
Alexander H. Le
- NIH
- National Institutes of Health, Bethesda
- National Institutes of Health
External person
H. Shimomura
External person
A. Lim
External person
E. S. Schroers
External person
S. I. Pascual Pascual
External person
Norma Romero
External person
M. de Los Angeles Tormos Munoz
External person
Jacinda Sampson
External person
S. Garcia Guixot
External person
Jaya Punetha
- George Washington University
- Department of Integrative Systems Biology
- Children's National Medical Center
- Icahn School of Medicine at Mount Sinai
- Baylor College of Medicine
External person
Monkol Lek
- Harvard University
- Broad Institute
- Analytic and Translational Genetics Unit
- Medical and Population Genetics Program
- Massachusetts Institute of Technology
- Program in Medical and Population Genetics
- Massachusetts General Hospital
External person
Sonia Canún
- Hospital General Dr. Manuel Gea González
- Universidad Nacional Autónoma de México
- Department de Genetica
- Hospital General "Dr. Manuel Gea González"
External person
M. Popolizio
External person
Thomas K. Koch
- San Francisco School of Medicine
- University of California at San Francisco
- Departments of Pediatrics and Neurology
External person
W. W. Bryant
- Scottish Rite Hospital
- University of Texas Southwestern Medical Center
- Department of Neurology
External person
H. W. Choi
External person
A. Bielsky
External person
P. Tacchetti
External person
Khurram Bashir
- University Hospital
- University of Alabama at Birmingham
- UAB Health System
External person
Hugo A. Sampaio
- Department of Neurology
- University of New South Wales
- Sydney Children's Hospital
- School of Women's and Children's Health
External person
Daniel E. Michele
- University of Iowa
- Howard Hughes Medical Institute
- Department of Molecular and Integrative Physiology
- University of Michigan, Ann Arbor
External person
Janice R. Anderson
- Addenbrooke's Hospital
- Department of Histopathology
- Cambridge University Hospitals NHS Foundation Trust
External person
A. A. Karaduman
External person
Kim S. Lau
- Univ. Texas-Southwestern Med. Ctr.
- Southwestern Med. Center at Dallas
- The University of Texas Southwestern Medical Center
- The University of Texas Southwestern Medical School
- Univ. Texas Southwestern Med. Ctr.
- University of Texas Southwestern Medical Center
- Southwestern Medical Center at Dallas
- Univ. of TX Southwestern Med. Ctr.
- Univ of Texas Southwestern Med. Ctr.
- Case Western Reserve University
- Southwestern Medical School
- Univ. Texas Southwestern Med. C.
- Univ. TX Southwestern Med. Ctr. D.
- Univ. of Texas Southwestern Med. C.
- Southwestern Medical Center
- UT Southwestern Medical Center
- Department of Physiology
- Department of Biochemistry
- Division of General Pediatrics
- Depts. of Pediatrics and Physiology
- Department of Internal Medicine
- Department of Veterans Affairs
- Department of Medicine
- University of Texas at Dallas
- Departments of Physiology
External person
S. P. Robertson
External person
E. Kenny
- Children's Hospital at Westmead
- University of Sydney
- Respiratory Support Service
External person
K. Mathews
External person
M. Srour
External person
P. M. Ingelmo
External person
L. J. Forman
- Texas Scottish Rite Hospital For Children
- Texas Scottish Rite Children Hosp.
- Texas Scottish Rite Hospital for Children
- Texas Scottish Rite Hosp. for Child.
- Departments of Laboratory and Neurology
- Scottish Rite Hospital for Children
External person
Ronald G. Victor
- Heart Institute
- D. W. R. Cardiovasc. Clin. Res. Ctr.
- University of Texas at Southwestern Medical Center
- Univ. Texas Southwestern Med. Ctr.
- Cedars-Sinai Medical Center
- NYC Poison Control Center
- University Hosp. of Copenhagen
- Division of Hypertension
- Univ. Texas Southwestern Med. Center
- Presbyterian Hospital of Dallas
- University of Texas Southwestern Medical Center
- University of Copenhagen
- 5323 Harry Hines Blvd., Dallas, T.
- University of Texas at Dallas
- U.T. Southwestern Medical Center
- U. T. Southwestern Medical Center
- Donald W. Reynolds Clinical Research Center
- Univ. of Texas SW Medical Center
- Univ. Texas-Southwestern Med. Ctr.
- The Cedars-Sinai Heart Institute
- University of Texas Southwestern
- Donald W. Reynolds Cardiovascular Clinical Research Center
- New York University
- University of Texas Southwestern Medical Center
- University of California at Los Angeles
- Cedars-Sinai Medical Center
- Division of Cardiology
- University of Texas at Austin
- Department of Internal Medicine
- Heart Institute
- Department of Internal Medicine
- Donald W. Reynolds Cardiovascular Clinical Research Center
- Department of Internal Medicine
- Department of Medicine
- Department of Medicine
- Division of Nutrition and Metabolic Diseases
- Department of Neurology
- Ryburn Ctr. for Molecular Cardiology
- Division of Translational Research
- Inst. for Exercise and Environ. Med.
- Divisions of Epidemiology
- Div. N
- Department of Medicine
- Hypertension Center
- Department of Internal Medicine
- Division of Hypertension
- Department of Medicine
- Division of Nephrology
- Division of Cardiology
- Harry S. Moss Heart Center
- The Moss Heart Center
- Division of Cardiology/Hypertension Section
- Department of Internal Medicine
- Department of Anaesthesia
- Division of Hematology-Oncology
- Hypertension Division
- Hypertension Center
- Texas Health Presbyterian Hospital Dallas
- NYC Poison Control Center
- Donald W. Reynolds Cardiovascular Clinical Research Center
External person
Adam Bournazos
- Discipline of Child and Adolescent Health
- Institute for Neuroscience and Muscle Research
- University of Sydney
- The Children's Hospital at Westmead
External person
Agnieszka Stępień
External person
Rabi Tawil
- University of Rochester
- Department of Neurology
- Department of Neurology
- Department ofNeurology
- University of Miami
- Department of Neurology
- The Pediatric Neuromuscular Clinical Research Network
External person
Michael B A Oldstoned
- Medical College of Georgia
- Scripps Research Institute
- Department of Neuropharmacology
- Inst. of Molec. Med. and Genetics
- Augusta University
- University of Florida
External person
M. Krüger
External person
Bettie Sue S Masters
- Univ. of Texas Health Science Center
- University of Texas Southwestern Medical Center
- University of Texas at San Antonio
- Medical College of Wisconsin
- University of Texas Health Science Center at San Antonio
- Department of Biochemistry
- Department of Biochemistry
- Dept. of Physiology
- Healih Science Cenier
- Department of Surgery
- Medical College of Wisconsin
External person
Annie Aloysius
- HPC
- Hammersmith Hospital
- Imperial College London
- Imperial College Healthcare NHS Trust
External person
Steven Greenberg
- Department of Neurology
- Harvard University
- Department of Neurology
- Cardiovascular Medical Specialists
- Celgene Corporation
- Brigham and Women’s Hospital
- Massachusetts General Hospital
External person
S. Gilabert
External person
Jocelyn Laporte
- University of Strasbourg
- Université de Strasbourg
- Université de Strasbourg
- Department of Translational Medicine
- INSERM U964
- University of Michigan, Ann Arbor
External person