Network
University of Texas Southwestern Medical Center
Organizational unit: University
Center for Alzheimer's and Neurodegenerative Diseases
Organizational unit: Department
NE-Lab Pascual
Organizational unit: Division
Peter O'Donnell Jr. School of Public Health
Organizational unit: Department
OP-Lab Hulleman
Organizational unit: Division
University of North Carolina at Chapel Hill
External organization: Academic
Author National Institutes of Health National Institutes of Health National Institutes of Health
External organization: Unknown
University of Texas Southwestern Medical Center
External organization: Academic
National Institute of Neurological Disorders and Stroke
External organization: Unknown
Research to Prevent Blindness
External organization: Unknown
Queen's University Kingston
External organization: Academic
National Cancer Institute-Navy Medical Oncology Branch, National Cancer Institute, Naval Hospital
External organization: Unknown
University of Pennsylvania
External organization: Academic
University of Toronto
External organization: Academic
National Institute of Allergy and Infectious Diseases , Food Allergy Initiative
External organization: Unknown
National Institutes of Health
External organization: Government
New Hope Research Foundation
External organization: Unknown
Hannah’s Hope Fund
External organization: Unknown
National Institute for Child Health and Human Development
External organization: Unknown
Emory University
External organization: Academic
University of Otago
External organization: Academic
Lincoln University
External organization: Academic
Taysha Gene Therapies
External organization: Unknown
Justus Liebig University Giessen
External organization: Academic
University of Manitoba
External organization: Academic
University of Illinois at Chicago
External organization: Academic
Rett Syndrome Research Trust
External organization: Unknown
University of Florida
External organization: Academic
Ohio State University
External organization: Academic
Unknown
External organization: Unknown
Tanta University
External organization: Academic
Vanderbilt University
External organization: Academic
Rare Trait Hope Fund
External organization: Unknown
International Rett Syndrome Foundation
External organization: Unknown
University of Glasgow
External organization: Academic
Harvard University
External organization: Academic
Nationwide Children’s Hospital
External organization: Medical
Carolina Institute for Developmental Disabilities
External organization: Unknown
Duke University
External organization: Academic
University of North Carolina
External organization: Unknown
Jackson Laboratory
External organization: Government
Rush University
External organization: Academic
University of Medicine and Dentistry of New Jersey
External organization: Academic
Children's National Medical Center
External organization: Medical
Hannah's Hope Fund
External organization: Unknown
University of California at San Diego
External organization: Academic
Washington University St. Louis
External organization: Academic
University of South Carolina
External organization: Academic
Johns Hopkins University
External organization: Academic
UCRF
External organization: Unknown
Queen's University and Cure Tay-Sachs Foundation
External organization: Unknown
Baylor College of Medicine
External organization: Academic
Legacy of Angels Foundation
External organization: Unknown
Novartis
External organization: Unknown
University of Michigan, Ann Arbor
External organization: Academic
University of Pittsburgh
External organization: Academic
National Institutes of Health National Institute for Environmental Health Sciences
External organization: Unknown
University of Wisconsin-Madison
External organization: Academic
Icahn School of Medicine at Mount Sinai
External organization: Academic
Jasper Against Batten Foundation
External organization: Unknown
Toronto Metropolitan University
External organization: Academic
Seoul National University
External organization: Academic
National Institute of Mental Health/National Institutes of Health
External organization: Unknown
Colorado State University
External organization: Academic
Canterbury Medical Research Foundation
External organization: Unknown
Batten Disease Support and Research Association
External organization: Unknown
University of California at San Francisco
External organization: Academic
Senator Paul D. Wellstone Muscular Dystrophy Cooperative Research Center
External organization: Unknown
Neurogene Inc.
External organization: Unknown
The Children's Hospital of Philadelphia
External organization: Medical
Ghent University
External organization: Academic
Lund University
External organization: Academic
Columbia University
External organization: Academic
University of California at Davis
External organization: Academic
NINDS/NIH
External organization: Unknown
College of Medical
External organization: Unknown
Pfizer Canada
External organization: Unknown
Angelman Syndrome Foundation
External organization: Unknown
Kingston General Hospital
External organization: Unknown
Canadian Institute of Health Research
External organization: Unknown
Vitreoretinal Associates
External organization: Unknown
University of Ferrara
External organization: Academic
National Institutes of Health, Bethesda
External organization: Unknown
Taysha Gene Therapies Inc.
External organization: Unknown
U.S. Army Breast Cancer Research Program
External organization: Unknown
Roche
External organization: Unknown
RProject A.L.S./Jenifer Estess Laboratory for Stem Cell Research
External organization: Unknown
Vlaams Instituut voor Biotechnologie
External organization: Unknown
Quest Diagnostics, Athena Brand
External organization: Unknown
National Center for Research Resources
External organization: Unknown
Chief Scientist Office
External organization: Unknown
McMaster & Heap Veterinary Practice
External organization: Unknown
Vaincre l’AGU foundation
External organization: Unknown
Oregon Health and Science University
External organization: Unknown
NICHD/NIH
External organization: Unknown
Hereditary Neuropathy Foundation
External organization: Unknown
Hacettepe University
External organization: Academic
NCBT
External organization: Unknown
NIH1K08AR054903-01A2 and Grayson Jockey Club Foundation
External organization: Unknown
National Institutes of Health
External organization: Unknown
Tulane University
External organization: Academic
Boston Children's Hospital
External organization: Medical
Gene Therapy Center
External organization: Unknown
Canadian Glycomics Network
External organization: Unknown
Albert Einstein College of Medicine
External organization: Unknown
Bowles Center for Alcohol Studies, University of North Carolina at Chapel Hill
External organization: Unknown
Asklepios BioPharmaceutical
External organization: Unknown
New York Stem Cell Foundation
External organization: Unknown
SpringWorks Therapeutics
External organization: Unknown
LLC
External organization: Unknown
Sanofi
External organization: Unknown
Batten Disease New Zealand
External organization: Unknown
Spark Therapeutics/Roche
External organization: Unknown
Collaborative Drug Discovery
External organization: Unknown
Association Européenne contre les Leucodystrophies
External organization: Unknown
Homology Medicines
External organization: Corporate
Cure CMT4J/Talia Duff Foundation
External organization: Unknown
National Institute of Environmental Health Sciences
External organization: Unknown
Michael J. Fox Foundation for Parkinson's Research
External organization: Unknown
University of Göttingen
External organization: Academic
Oregon National Primate Research Center
External organization: Unknown
Auburn University
External organization: Academic
Rett Syndrome Association
External organization: Unknown
Batten Hope Foundation
External organization: Unknown
Burke-Cornell Medical Research Institute
External organization: Unknown
Queen's University
External organization: Unknown
Sio Gene Therapies
External organization: Unknown
Medical College of Wisconsin
External organization: Academic
Advanced Foods and Materials Canada
External organization: Unknown
Center for Precision Genetics at The Jackson Laboratory
External organization: Unknown
CURE Childhood Cancer
External organization: Unknown
Canadian Institutes of Health Research
External organization: Government
Rosetrees Trust
External organization: Unknown
R.S. MacDonald Charitable Trust
External organization: Unknown
Delmar
External organization: Unknown
Oregon Health and Science University
External organization: Academic
Rady Children’s Institute for Genomic Medicine
External organization: Unknown
BridgeBio
External organization: Unknown
Mila’s Miracle Foundation
External organization: Unknown
Department of Microbiology and Immunology
External organization: Unknown
Jaguar Therapeutics
External organization: Unknown
Maurice and Phyllis Paykel Trust
External organization: Unknown
University Pennsylvania
External organization: Unknown
NINDS Center
External organization: Unknown
UT Southwestern Medical Center Diagnostic Laboratory
External organization: Unknown
University of Eastern Finland
External organization: Academic
Genzyme
External organization: Unknown
Spastic Paraplegia Foundation
External organization: Unknown
New Hope Research Foundation in North Oaks
External organization: Unknown
Ferring Ventures
External organization: Unknown
Howard Hughes Medical Institute
External organization: Academic
California Primate Research Center
External organization: Unknown
University of Rochester
External organization: Academic
Greenwood Genetics Center
External organization: Unknown
Université de Bordeaux
External organization: Academic
Rowan University
External organization: Academic
Rose F. Kennedy Intellectual and Developmental Disabilities Research Center
External organization: Unknown
Universidad de Buenos Aires
External organization: Academic
Division of Health Sciences, University of Otago
External organization: Unknown
Novartis Gene Therapies
External organization: Unknown
Division of Hematology and the Perelman Center for Cellular and Molecular Therapeutics
External organization: Unknown
UNC Center for Animal MRI
External organization: Unknown
Friedrich-Alexander University Erlangen-Nürnberg
External organization: Academic
NIH Office of the Director
External organization: Unknown
Université Laval
External organization: Academic
Hannah’s Hope Fund for Giant Axonal Neuropathy
External organization: Unknown
Morton Fichtenbaum Charitable Trust
External organization: Unknown
University of Connecticut
External organization: Academic
Asklepios Biopharma, Neurogene, Abeona Therapeutics
External organization: Unknown
UNC IDDRC
External organization: Unknown
TrialSpark, Inc.
External organization: Unknown
Edgewise Therapeutics and Sarepta Therapeutics
External organization: Unknown
Ultragenyx Pharmaceutical Inc.
External organization: Corporate
David H. Murdock Research Institute
External organization: Unknown
Spark Therapeutics
External organization: Corporate
NYVAX Inc.
External organization: Unknown
Amyotrophic Lateral Sclerosis Association
External organization: Unknown
Takeda California, Inc.
External organization: Unknown
Vanderbilt-Ingram Cancer Center, Vanderbilt University Medical Center
External organization: Unknown
Gabrielle’s Angels Foundation
External organization: Unknown
Biology and Information Science Programs
External organization: Unknown
Lineberger Comprehensive Cancer Center
External organization: Unknown
Collaborations in Chemistry
External organization: Unknown
MSA Coalition
External organization: Unknown
The Mind Research Network
External organization: Unknown
Parkinson's Disease Foundation
External organization: Unknown
VA Medical Center
External organization: Medical
Arnold Consultancy and Technology LLC
External organization: Unknown
Case Western Reserve University
External organization: Academic
Asklepios BioPharmaceutical, Inc.
External organization: Corporate
Texas Children's Hospital Houston
External organization: Medical
Biogen IDEC
External organization: Corporate
CureAP4 Foundation
External organization: Unknown
Ultragenyx and Hope for ULD
External organization: Unknown
Center for Neurodegenerative Science
External organization: Unknown
National Institute of Alcohol Abuse and Alcoholism
External organization: Unknown
Saliogen Therapeutics
External organization: Unknown
Biogen
External organization: Unknown
University of Edinburgh
External organization: Academic
Qatar Science & Technology Park
External organization: Academic
Howard Hughes Medical Institute
External organization: Unknown
Northwestern University
External organization: Academic
Inhibikase Therapeutics, Inc.
External organization: Unknown
Administrative Headquarters of the Max Planck Society
External organization: Government
University of Washington
External organization: Academic
CureSPG50 Foundation
External organization: Unknown
Jackson Laboratories
External organization: Unknown
University of South Alabama
External organization: Academic
Wadsworth Center for Laboratories and Research
External organization: Government
Muscular Dystrophy Association
External organization: Unknown
Van Sickle Family Foundation Inc.
External organization: Unknown
CAMRI
External organization: Unknown
St. Joseph's Hospital and Medical Center, Phoenix
External organization: Medical
Washington National Primate Research Center
External organization: Unknown
UT Southwestern Metabolic
External organization: Unknown
AFM-Téléthon
External organization: Unknown
Thomas Jefferson University
External organization: Academic
Bowles Center for Alcohol Studies
External organization: Unknown
University of Massachusetts Medical School
External organization: Academic
Abeona Therapeutics and Taysha Gene Therapies
External organization: Unknown
Queen’s University in Kingston, ON, Canada
External organization: Unknown
CHU Hôpitaux de Rouen
External organization: Medical
University of Oxford
External organization: Academic
Biomarin Pharmaceuticals Inc.
External organization: Unknown
UNC University
External organization: Unknown
Saint Louis University
External organization: Academic
Rett Syndrome Research Trust Gene Therapy Consortium
External organization: Unknown
Neural Stem Cell Institute
External organization: Unknown
Cure SURF1 Foundation
External organization: Unknown
Institut des Maladies Neurodégénératives
External organization: Unknown
Sarepta Therapeutics
External organization: Corporate
National Cancer Institute
External organization: Unknown
Asklepios Biopharma
External organization: Unknown
New York State Stem Cell Science
External organization: Unknown
Sinnett Laboratory
External organization: Unknown
Grayson Jockey Club Foundation
External organization: Unknown
CureKids NZ
External organization: Unknown
NIH-NICHD Intellectual and Developmental Disabilities Research Center Support
External organization: Unknown
Cure Mito Foundation
External organization: Unknown
Astellas Pharma
External organization: Unknown
Erasmus University Rotterdam
External organization: Academic
Asklepios BioPharmaceutical Inc.
External organization: Unknown
Queen?s University in Kingston, ON, Canada
External organization: Unknown
Amicus Therapeutics
External organization: Unknown
Cornell University
External organization: Academic
Israel National Road Safety Authority
External organization: Unknown
Quorum Consulting, Inc.
External organization: Unknown