Network
University of Texas Southwestern Medical Center
Organizational unit: University
BP-Lab Rizo-Rey
Organizational unit: Division
CRI-Lab Prashant Mishra
Organizational unit: Division
NE-Lab Pascual
Organizational unit: Division
CRI - Lab Regina Shin
Organizational unit: Division
Peter O'Donnell Jr. School of Public Health
Organizational unit: Department
Neurology & Neurotherapeutics - NE Neuro Pediatrics Section
Organizational unit: Division
Cecil H. and Ida Green Center For Reproductive Biology Sciences
School of Medicine, GN-Lab A. Solmonson
Organizational unit: Department
SPH-Data Sciences in Precision
Peter O'Donnell Jr. School of Public Health
Organizational unit: Division
Neurology & Neurotherapeutics - NE Neuro Muscular Section
Organizational unit: Division
GN-Lab A. Solmonson
Organizational unit: Division
Children's Research Institute
Children's Medical Center Research Institute At Ut Southwestern
Organizational unit: Division
University of Texas Southwestern Medical Center
External organization: Academic
National Institutes of Health
External organization: Government
Oregon Health and Science University
External organization: Academic
BioMarin Pharmaceutical
External organization: Unknown
Aeglea BioTherapeutics
External organization: Unknown
Cooper University Health Care
External organization: Academic
Tulane University
External organization: Academic
Boston Children's Hospital
External organization: Medical
Children's Hospital of Michigan
External organization: Medical
Horizon Therapeutics
External organization: Unknown
University of Utah
External organization: Academic
National Institute of Diabetes and Digestive and Kidney Diseases
External organization: Unknown
Harvard University
External organization: Academic
University of Texas Health Science Center at Houston
External organization: Academic
PLLC
External organization: Unknown
Children's National Medical Center
External organization: Medical
University of Texas Medical Branch at Galveston
External organization: Academic
BioMarin Pharmaceutical Inc.
External organization: Corporate
Indiana University Bloomington
External organization: Academic
Children's Memorial Hospital
External organization: Medical
NOVA University Lisbon
External organization: Academic
Children's Medical Center Research Institute
External organization: Unknown
University of Toronto
External organization: Academic
Inc.
External organization: Unknown
Jill Skrabal
External organization: Unknown
LifeDiet
External organization: Unknown
National Institutes of Health, Bethesda
External organization: Unknown
Bristol-Myers Squibb
External organization: Corporate
Kwandong University
External organization: Academic
St. Christopher's Hospital for Children
External organization: Medical
Stanford University
External organization: Academic
Vitaflo International Ltd
External organization: Unknown
University of South Florida
External organization: Academic
Once Upon A Time Foundation
External organization: Unknown
Wayne State University
External organization: Academic
Chung Lee, MD
External organization: Unknown
Hacettepe University
External organization: Academic
Peking University
External organization: Unknown
Centro Hospitalar Universitário de São João
External organization: Medical
BioMarin and Homology Medicines
External organization: Unknown
City of Hope National Med Center
External organization: Medical
National Heart Lung and Blood Institute
External organization: Unknown
Sanofi
External organization: Unknown
Shire
External organization: Unknown
University of Santiago de Compostela
External organization: Academic
Homology Medicines
External organization: Corporate
University of Lisbon
External organization: Academic
Rhythm Pharmaceuticals
External organization: Unknown
Individual with PKU
External organization: Unknown
University of Michigan, Ann Arbor
External organization: Academic
University of Pittsburgh
External organization: Academic
Individual with PKU
External organization: Unknown
Icahn School of Medicine at Mount Sinai
External organization: Academic
University of Melbourne
External organization: Academic
Mount Sinai Hospital Medical Center
External organization: Medical
Howard Hughes Medical Institute
External organization: Academic
University of Hamburg
External organization: Academic
Cycle Therapeutics
External organization: Unknown
University of California at Irvine
External organization: Academic
Atlantic Health
External organization: Unknown
Applied Therapeutics
External organization: Unknown
Department of Medicine
External organization: Unknown
LogicBio Pharmaceuticals
External organization: Unknown
RehabMetrics
External organization: Unknown
University of Kentucky
External organization: Academic
Meso Scale Discovery
External organization: Unknown
CRI Metabolomics Facility
External organization: Unknown
Sangamo Therapeutics
External organization: Unknown
University of Florida
External organization: Academic
Alnylam
External organization: Unknown
Drexel University
External organization: Academic
University of South Dakota
External organization: Academic
Florey Institute of Neuroscience and Mental Health
External organization: Academic
Great Ormond Street Hospital for Children Foundation Trust
External organization: Unknown
Howard Hughes Medical Institute
External organization: Unknown
Hospital Ramon y Cajal
External organization: Medical
Northwestern University
External organization: Academic
University of Mississippi
External organization: Academic
Children’s Medical Research Institute
External organization: Unknown
Inventiva Pharma
External organization: Unknown
Takeda Pharmaceuticals U.S.A.
External organization: Unknown
University of Washington
External organization: Academic
University of Missouri
External organization: Academic
Regeneron Pharmaceuticals, Inc.
External organization: Corporate
Universidade Estadual do Ceará
External organization: Academic
U.S. Public Health Service
External organization: Unknown
Welch Foundation
External organization: Unknown
National Institute for Child Health and Human Development
External organization: Unknown
Cancer Prevention and Research Institute of Texas
External organization: Unknown
Division of General Pediatrics, Department of Pediatrics, UT Southwestern Medical Center
External organization: Unknown
Phoenix Children's Hospital
External organization: Medical
University of Colorado Anschutz Medical Campus
External organization: Academic
Author National Institutes of Health National Institutes of Health National Institutes of Health
External organization: Unknown
University Health Network
External organization: Medical
Rutgers - The State University of New Jersey, New Brunswick
External organization: Academic
Royal Melbourne Hospital
External organization: Medical
Astellas Pharma
External organization: Unknown
Amicus Therapeutics
External organization: Unknown
Denali Therapeutics
External organization: Unknown
Leiden University
External organization: Academic