Toward RNAi therapy for the polyglutamine disease Machado-Joseph disease

Maria Do Carmo Costa, Katiuska Luna-Cancalon, Svetlana Fischer, Naila S. Ashraf, Michelle Ouyang, Rahil M. Dharia, Lucas Martin-Fishman, Yemen Yang, Vikram G. Shakkottai, Beverly L. Davidson, Edgardo Rodríguez-Lebrón, Henry L. Paulson