The 10th Oligonucleotide Therapy Approved: Golodirsen for Duchenne Muscular Dystrophy

Annemieke Aartsma-Rus, David R. Corey

Research output: Contribution to journalReview articlepeer-review

79 Scopus citations
Original languageEnglish (US)
Pages (from-to)67-70
Number of pages4
JournalNucleic Acid Therapeutics
Volume30
Issue number2
DOIs
StatePublished - Apr 2020

ASJC Scopus subject areas

  • Biochemistry
  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Drug Discovery

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