Precise genomic editing of pathogenic mutations in RBM20 rescues dilated cardiomyopathy

Takahiko Nishiyama, Yu Zhang, Miao Cui, Hui Li, Efrain Sanchez-Ortiz, John R. McAnally, Wei Tan, Jiwoong Kim, Kenian Chen, Lin Xu, Rhonda Bassel-Duby, Eric N. Olson

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Medicine & Life Sciences