Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy

Research output: Contribution to journalArticlepeer-review

184 Scopus citations
Original languageEnglish (US)
Pages (from-to)497-499
Number of pages3
JournalNature neuroscience
Volume20
Issue number4
DOIs
StatePublished - Mar 29 2017

ASJC Scopus subject areas

  • General Neuroscience

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