Friedreich's ataxia induced pluripotent stem cells model intergenerational GAATTC triplet repeat instability

Sherman Ku, Elisabetta Soragni, Erica Campau, Elizabeth A. Thomas, Gulsah Altun, Louise C. Laurent, Jeanne F. Loring, Marek Napierala, Joel M. Gottesfeld

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186 Scopus citations

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Medicine & Life Sciences