Biochemistry, Genetics and Molecular Biology
Gene Therapy
100%
Adeno Associated Virus
55%
Transgene
35%
Transfer Gene
31%
Mouse
30%
Serotype
25%
Hexosaminidase
25%
GM2 Gangliosidoses
24%
Mouse Model
23%
GM2 (Ganglioside)
23%
Adeno Associated Virus Vector
20%
Virus Vector
19%
Clinical Trial
18%
Sandhoff Disease
18%
Capsid
17%
Galactosylceramidase
17%
Batten Disease
15%
Neuronal Ceroid Lipofuscinosis
15%
Drug Megadose
14%
Promoter Region
14%
Krabbe Disease
14%
Enzyme
13%
Knockout Mouse
12%
Immune Response
11%
Rett Syndrome
11%
HEXA
11%
MECP2
11%
Enzymatic Hydrolysis
10%
Gene Expression
10%
Animal Model
10%
Genetic Disorder
10%
Gigaxonin
9%
Immunomodulation
9%
Lysosomal Storage Disease
9%
Lifespan
9%
Tay-Sachs Disease
8%
Expression Cassette
8%
Gene Delivery
7%
Low Drug Dose
7%
T Cell
7%
Motor Performance
7%
Gene Targeting
7%
Neutralizing Antibody
7%
Regulatory Element
7%
DNA Replication
6%
Twitcher Mouse
6%
Protein Expression
6%
Equine Model
6%
Intermediate Filament
6%
Wild Type Mouse
6%
Neuroscience
Adeno-Associated Virus
77%
Intrathecal
56%
Adeno Associated Virus Vector
46%
Central Nervous System
44%
Gene Transfer
36%
Peripheral Neuropathy
33%
Gene Delivery
23%
Rett Syndrome
21%
Promoter Region
21%
Motor Neuron
20%
Nervous System Disorder
18%
Galactosylceramidase
17%
Krabbe Disease
17%
Neurological Disorder
17%
N4 (Beta N Acetylglucosaminyl)asparaginase
15%
Transgene
15%
Virus Gene
14%
Neurodegenerative Disorder
13%
MECP2
13%
Methyl CpG Binding Protein 2
13%
Gene Expression
12%
Virus Vector
12%
Leukodystrophy
12%
Oligodendrocyte
12%
Neuronal Ceroid Lipofuscinosis
11%
In Vivo
11%
Psychosine
10%
Beta N Acetylhexosaminidase
9%
Multiple System Atrophy
9%
Cisterna Magna
9%
Blood Brain Barrier
8%
Alpha-Synuclein
8%
Adverse Effect
8%
Aspartoacylase
8%
T Cell
8%
Neurodegeneration
7%
Stem Cell
7%
Neurodevelopmental Disorder
7%
Peripheral Nervous System
7%
Neutralizing Antibody
6%
Canavan Disease
6%
Myelinogenesis
6%
Brain Disease
6%
Viral Gene Delivery System
5%
Ganglioside GM2
5%
Nervous System
5%
Glia
5%
Hematopoietic Stem Cell
5%
White Matter Disease
5%
In Vitro
5%
Keyphrases
Gene Therapy
79%
Central Nervous System
25%
Giant Axonal Neuropathy
19%
AAV9
18%
GM2 Gangliosidosis
16%
Gene Transfer
14%
Adenovirus
12%
Intrathecal
12%
GM2 Ganglioside
12%
Globoid Cell Leukodystrophy
12%
Clinical Translation
12%
Adeno-associated Viral Vector
12%
Methyl-CpG-binding Protein 2 (MeCP2)
11%
Mouse Model
11%
Rett Syndrome
10%
Adeno-associated Viral
10%
Gigaxonin
10%
Aspartylglucosaminuria
10%
Adeno-associated Virus Serotype 9
10%
Viral Vectors
10%
AB Variant
10%
Batten Disease
10%
Genetic Disease
10%
Neurological Disorders
9%
Self-complementary Adeno-associated Virus
9%
Aspartylglucosaminidase
9%
SURF1
9%
Recombinant Adeno-associated Virus (rAAV)
9%
Systems Genetics
9%
High Dose
9%
Lysosomal Storage Disease
9%
Galactosylceramidase
8%
Neurodegenerative Diseases
8%
Motor Neuron
8%
Self-complementary
7%
Neurodevelopmental Disorders
7%
Serotype 9
7%
Immune Response
7%
Krabbe Disease
7%
Intrathecal Delivery
7%
Psychosine
7%
GM2 Activator Protein
6%
Seizure
6%
Vector Design
6%
Sandhoff Disease
6%
Knock-in Mouse Model
6%
Peripheral Nervous System
6%
Gene Expression
6%
MECP2 Gene
6%
AAV9 Gene Therapy
5%
